日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Neutralizing Antibodies: Role in Immune Response and Viral Vector Based Gene Therapy

中和抗体:在免疫反应和基于病毒载体的基因治疗中的作用

Tsaregorodtseva, Tatiana S; Gubaidullina, Aigul A; Kayumova, Beata R; Shaimardanova, Alisa A; Issa, Shaza S; Solovyeva, Valeriya V; Sufianov, Albert A; Sufianova, Galina Z; Rizvanov, Albert A

Increasing β-hexosaminidase A activity using genetically modified mesenchymal stem cells

利用转基因间充质干细胞提高β-己糖胺酶A活性

Alisa A Shaimardanova, Daria S Chulpanova, Valeriya V Solovyeva, Shaza S Issa, Aysilu I Mullagulova, Angelina A Titova, Yana O Mukhamedshina, Anna V Timofeeva, Alexander M Aimaletdinov, Islam R Nigmetzyanov, Albert A Rizvanov

Growth Factors and Their Application in the Therapy of Hereditary Neurodegenerative Diseases

生长因子及其在遗传性神经退行性疾病治疗中的应用

Issa, Shaza; Fayoud, Haidar; Shaimardanova, Alisa; Sufianov, Albert; Sufianova, Galina; Solovyeva, Valeriya; Rizvanov, Albert

Various AAV Serotypes and Their Applications in Gene Therapy: An Overview

各种AAV血清型及其在基因治疗中的应用:概述

Issa, Shaza S; Shaimardanova, Alisa A; Solovyeva, Valeriya V; Rizvanov, Albert A

Safety and Efficacy of Intravenous and Intrathecal Delivery of AAV9-Mediated ARSA in Minipigs

在小型猪中静脉和鞘内注射 AAV9 介导的 ARSA 的安全性和有效性

Aysilu Mullagulova, Alisa Shaimardanova, Valeriya Solovyeva, Yana Mukhamedshina, Daria Chulpanova, Alexander Kostennikov, Shaza Issa, Albert Rizvanov

Functionality of a bicistronic construction containing HEXA and HEXB genes encoding β-hexosaminidase A for cell-mediated therapy of GM2 gangliosidoses

含有编码 β-己糖胺酶 A 的 HEXA 和 HEXB 基因的双顺反子结构在 GM2 神经节苷脂沉积症的细胞介导治疗中的功能

Alisa A Shaimardanova, Daria S Chulpanova, Valeriya V Solovyeva, Aleksandr M Aimaletdinov, Albert A Rizvanov

Current Strategies for the Gene Therapy of Autosomal Recessive Congenital Ichthyosis and Other Types of Inherited Ichthyosis

目前针对常染色体隐性遗传性先天性鱼鳞病和其他类型遗传性鱼鳞病的基因治疗策略

Chulpanova, Daria S; Shaimardanova, Alisa A; Ponomarev, Aleksei S; Elsheikh, Somaia; Rizvanov, Albert A; Solovyeva, Valeriya V

Mesenchymal Stem Cell-Based Therapy for Lysosomal Storage Diseases and Other Neurodegenerative Disorders

间充质干细胞疗法治疗溶酶体贮积症和其他神经退行性疾病

Issa, Shaza S; Shaimardanova, Alisa A; Valiullin, Victor V; Rizvanov, Albert A; Solovyeva, Valeriya V

Serum Cytokine Profile, Beta-Hexosaminidase A Enzymatic Activity and GM(2) Ganglioside Levels in the Plasma of a Tay-Sachs Disease Patient after Cord Blood Cell Transplantation and Curcumin Administration: A Case Report

脐带血细胞移植和姜黄素治疗后泰-萨克斯病患者血浆中细胞因子谱、β-己糖胺酶A酶活性和GM(2)神经节苷脂水平:病例报告

Shaimardanova, Alisa A; Chulpanova, Daria S; Solovyeva, Valeriya V; Garanina, Ekaterina E; Salafutdinov, Ilnur I; Laikov, Alexander Vladimirovich; Kursenko, Vadim V; Chakrabarti, Lisa; Zakharova, Ekaterina Yu; Bukina, Tatiana M; Baydakova, Galina V; Rizvanov, Albert Anatolyevich

Extracellular vesicles in the diagnosis and treatment of central nervous system diseases

细胞外囊泡在中枢神经系统疾病诊断和治疗中的应用

Shaimardanova, Alisa A; Solovyeva, Valeriya V; Chulpanova, Daria S; James, Victoria; Kitaeva, Kristina V; Rizvanov, Albert A