日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Base editing of key residues in the BCL11A-XL-specific zinc finger domains derepresses fetal globin expression

BCL11A-XL特异性锌指结构域关键残基的碱基编辑可解除胎儿珠蛋白表达的抑制。

Rajendiran, Vignesh; Devaraju, Nivedhitha; Haddad, Mahdi; Ravi, Nithin Sam; Panigrahi, Lokesh; Paul, Joshua; Gopalakrishnan, Chandrasekar; Wyman, Stacia; Ariudainambi, Keerthiga; Mahalingam, Gokulnath; Periyasami, Yogapriya; Prasad, Kirti; George, Anila; Sukumaran, Dhiyaneshwaran; Gopinathan, Sandhiya; Pai, Aswin Anand; Nakamura, Yukio; Balasubramanian, Poonkuzhali; Ramalingam, Rajasekaran; Thangavel, Saravanabhavan; Velayudhan, Shaji R; Corn, Jacon E; Mackay, Joel P; Marepally, Srujan; Srivastava, Alok; Crossley, Merlin; Mohankumar, Kumarasamypet M

Editing of homologous globin genes by nickase-deficient base editor mitigates large intergenic deletions in HSPCs

利用缺乏切口酶的碱基编辑器对同源珠蛋白基因进行编辑,可以减轻造血干细胞中大片段基因间缺失的影响。

George, Anila; Sadanandan, Poornasree; Ravi, Nithin Sam; Vaishnavi, B; Marepally, Srujan; Thangavel, Saravanbhavan; Velayudhan, Shaji R; Srivastava, Alok; Mohankumar, Kumarasamypet M

Ethereum blockchain for electronic health records: securing and streamlining patient management

以太坊区块链在电子健康记录中的应用:保障和简化患者管理

Mole, J S Simi; Shaji, R S

Editing the core region in HPFH deletions alters fetal and adult globin expression for treatment of β-hemoglobinopathies

通过编辑HPFH缺失的核心区域,可以改变胎儿和成人珠蛋白的表达,用于治疗β-血红蛋白病。

Vigneshwaran Venkatesan,Abisha Crystal Christopher,Manuel Rhiel,Manoj Kumar K Azhagiri,Prathibha Babu,Kaivalya Walavalkar,Bharath Saravanan,Geoffroy Andrieux,Sumathi Rangaraj,Saranya Srinivasan,Karthik V Karuppusamy,Annlin Jacob,Abhirup Bagchi,Aswin Anand Pai,Yukio Nakamura,Ryo Kurita,Poonkuzhali Balasubramanian,Rekha Pai,Srujan Kumar Marepally,Kumarasamypet Murugesan Mohankumar,Shaji R Velayudhan,Melanie Boerries,Dimple Notani,Toni Cathomen,Alok Srivastava,Saravanabhavan Thangavel

Modulating retinoid-X-receptor alpha (RXRA) expression sensitizes chronic myeloid leukemia cells to imatinib in vitro and reduces disease burden in vivo

调节视黄酸X受体α (RXRA) 的表达可使慢性粒细胞白血病细胞在体外对伊马替尼敏感,并在体内降低疾病负荷。

Bharathi M Rajamani,Raveen Stephen Stallon Illangeswaran,Esther Sathya Bama Benjamin,Balaji Balakrishnan,Daniel Zechariah Paul Jebanesan,Saswati Das,Aswin Anand Pai,Rakhi Thalayattu Vidhyadharan,Ajith Mohan,Sreeja Karathedath,Aby Abraham,Vikram Mathews,Shaji R Velayudhan,Poonkuzhali Balasubramanian

Efficient gene editing in induced pluripotent stem cells enabled by an inducible adenine base editor with tunable expression

通过可调节表达的诱导腺嘌呤碱基编辑器实现诱导多能干细胞中的高效基因编辑

Krittika Nandy, Dinesh Babu, Sonam Rani, Gaurav Joshi, Smitha Ijee, Anila George, Dhavapriya Palani, Chitra Premkumar, Praveena Rajesh, S Vijayanand, Ernest David, Mohankumar Murugesan, Shaji R Velayudhan

Identification of novel HPFH-like mutations by CRISPR base editing that elevate the expression of fetal hemoglobin

利用 CRISPR 碱基编辑技术鉴定可提高胎儿血红蛋白表达的新型 HPFH 样突变

Nithin Sam Ravi ,Beeke Wienert ,Stacia K Wyman ,Henry William Bell ,Anila George ,Gokulnath Mahalingam ,Jonathan T Vu ,Kirti Prasad ,Bhanu Prasad Bandlamudi ,Nivedhitha Devaraju ,Vignesh Rajendiran ,Nazar Syedbasha ,Aswin Anand Pai ,Yukio Nakamura ,Ryo Kurita ,Muthuraman Narayanasamy ,Poonkuzhali Balasubramanian ,Saravanabhavan Thangavel ,Srujan Marepally ,Shaji R Velayudhan ,Alok Srivastava ,Mark A DeWitt ,Merlin Crossley ,Jacob E Corn ,Kumarasamypet M Mohankumar

Efficient and error-free correction of sickle mutation in human erythroid cells using prime editor-2

使用 prime editor-2 高效无误地校正人类红系细胞中的镰状突变

Anila George, Nithin Sam Ravi, Kirti Prasad, Lokesh Panigrahi, Sanya Koikkara, Vignesh Rajendiran, Nivedhitha Devaraju, Joshua Paul, Aswin Anand Pai, Yukio Nakamura, Ryo Kurita, Poonkuzhali Balasubramanian, Saravanabhavan Thangavel, Srujan Marepally, Shaji R Velayudhan, Alok Srivastava, Kumarasamype

Erythroid lineage-specific lentiviral RNAi vectors suitable for molecular functional studies and therapeutic applications

适用于分子功能研究和治疗应用的红细胞谱系特异性慢病毒 RNAi 载体

Abhirup Bagchi #, Nivedhitha Devaraju #, Karthik Chambayil, Vignesh Rajendiran, Vigneshwaran Venkatesan, Nilofer Sayed, Aswin Anand Pai, Aneesha Nath, Ernest David, Yukio Nakamura, Poonkuzhali Balasubramanian, Alok Srivastava, Saravanabhavan Thangavel, Kumarasamypet M Mohankumar, Shaji R Velayudhan1

Gene Editing in Human Induced Pluripotent Stem Cells Using Doxycycline-Inducible CRISPR-Cas9 System

利用强力霉素诱导的 CRISPR-Cas9 系统对人类诱导性多能干细胞进行基因编辑

Vasanth Thamodaran, Sonam Rani, Shaji R Velayudhan