Rescue of DNA-PK Signaling and T-Cell Differentiation by Targeted Genome Editing in a prkdc Deficient iPSC Disease Model
在 prkdc 缺陷型 iPSC 疾病模型中通过靶向基因组编辑挽救 DNA-PK 信号传导和 T 细胞分化
期刊:PLoS Genetics
影响因子:
doi:10.1371/journal.pgen.1005239
Shamim H Rahman, Johannes Kuehle, Christian Reimann, Tafadzwa Mlambo, Jamal Alzubi, Morgan L Maeder, Heimo Riedel, Paul Fisch, Tobias Cantz, Cornelia Rudolph, Claudio Mussolino, J Keith Joung, Axel Schambach, Toni Cathomen