An 8-week, open-label, dose-finding study of nimodipine for the treatment of progranulin insufficiency from GRN gene mutations
一项为期 8 周、开放标签、剂量探索性研究,旨在评估尼莫地平治疗 GRN 基因突变引起的粒蛋白前体缺乏症的疗效。
期刊:Alzheimer's and Dementia: Translational Research and Clinical Interventions
影响因子:6.8
doi:10.1016/j.trci.2017.08.002
Sha, Sharon J; Miller, Zachary A; Min, Sang-Won; Zhou, Yungui; Brown, Jesse; Mitic, Laura L; Karydas, Anna; Koestler, Mary; Tsai, Richard; Corbetta-Rastelli, Chiara; Lin, Sophie; Hare, Emma; Fields, Scott; Fleischmann, Kirsten E; Powers, Ryan; Fitch, Ryan; Martens, Lauren Herl; Shamloo, Mehrdad; Fagan, Anne M; Farese, Robert V Jr; Pearlman, Rodney; Seeley, William; Miller, Bruce L; Gan, Li; Boxer, Adam L