Nebulized and intravenous enzyme replacement therapy in mice with mucopolysaccharidosis type II.
对患有 II 型粘多糖贮积症的小鼠进行雾化和静脉注射酶替代疗法
期刊:PLoS One
影响因子:2.6
doi:10.1371/journal.pone.0310485
Shamoun Alex J, Reis Gisienne, Ashley Malaica, Labilloy Anatalia, Ferreira Leonardo F