Spatially concentrated adenine base editors efficiently correct PLP1 mutations in oligodendrocytes.
空间集中的腺嘌呤碱基编辑器能有效纠正少突胶质细胞中的 PLP1 突变。
期刊:Nucleic Acids Research
影响因子:13.1
doi:10.1093/nar/gkag156
Zhang Chi, Ye Ke, Shang Yafang, Song Yixuan, Li Pingping, Jiang Xinyue, Yang Cuiping, Liang Aibin, Zhang Jian, Meng Feilong, Zhang Mingliang