日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Concizumab in hemophilia with inhibitors: longer-term efficacy and safety results from the phase 3 explorer7 study

Concizumab治疗伴有抑制剂的血友病:3期explorer7研究的长期疗效和安全性结果

Mahlangu, Johnny; Boban, Ana; Bruzelius, Maria; Castaman, Giancarlo; Hampton, Kingsley; Knoebl, Paul; Lebreton, Aurélien; Linari, Silvia; López-Jaime, Francisco-José; Martins Mazini Tavares, Camila; Nekkal, Mohamed Salim; Nogami, Keiji; Rhode Høgh Nielsen, Amalie; Shapiro, Amy; d'Oiron, Roseline

Acceptability and Determinants for Implementation of the EnzySystem, a Novel Near-Patient Testing Platform for Haemophilia A

EnzySystem(一种新型的甲型血友病床旁检测平台)的可接受性及其实施决定因素

Bavinck, Aernoud P; Davis, Kyle; van Engelshoven, Lisa; van Lier, Monique G; Hamacher, Tanja; Blijlevens, Nicole M A; Shapiro, Amy; Schols, Saskia E M; van Heerde, Waander L

Real-world adherence to and persistence with emicizumab in people with hemophilia A using a national claims database

利用国家索赔数据库评估A型血友病患者在真实世界中对艾美赛珠单抗的依从性和持续性

Lee, Janet S; Schuldt, Robert; Xia, Zhiyu; Lee, Lucy; Biondo, Juliana M L; Shapiro, Amy D

Reversing PAI-1 deficiency in blood using mRNA lipid nanoparticles.

利用mRNA脂质纳米颗粒逆转血液中PAI-1缺乏症

Ferraresso Francesca, Skaer Chad W, Badior Katherine, Pulente Serena M, Paul Manoj, Ketelboeter Laura, Chen Taylor H S, Cullis Pieter R, Gupta Sweta, Shapiro Amy, Mulvihill Erin E, Kastrup Christian J

Gynecologic and obstetric complications in women with congenital fibrinogen disorders: insights from the Prospective Rare Bleeding Disorders Database

先天性纤维蛋白原疾病女性的妇科和产科并发症:来自前瞻性罕见出血性疾病数据库的启示

Mohsenian, Samin; Palla, Roberta; Menegatti, Marzia; Cairo, Andrea; Siboni, Simona Maria; Neerman-Arbez, Marguerite; Karimi, Mehran; Pargantou, Helen; Asselta, Rosanna; Mikovic, Danijela; Saracevic, Marko; Laros-van Gorkom, Britta; Jacobs, Laura; Shapiro, Amy; Williamson, Adrianna; Makris, Michael; Casini, Alessandro; Peyvandi, Flora

Recombinant factor VIIa: new insights into the mechanism of action through product innovation

重组凝血因子VIIa:通过产品创新深入了解其作用机制

Escobar, Miguel A; Hoffman, Maureane; Castaman, Giancarlo; Hermans, Cedric; Mahlangu, Johnny; Oldenburg, Johannes; Percy, Charles L; Reding, Mark T; Shapiro, Amy D; Pipe, Steven W

Safety and Efficacy of Long-Term Treatment of Type 1 Plasminogen Deficient Patients With Intravenous Plasminogen Replacement Therapy

静脉注射纤溶酶原替代疗法治疗1型纤溶酶原缺乏症患者的安全性和有效性

Shapiro, Amy D; McDaniel, Heather; Decker, Robert W; Nakar, Charles; Lorber, Jeremy; Thukral, Neelam; Parker, Joseph M; Thibaudeau, Karen

Emerging Therapies in Hemophilia: Improving Equitable Access to Care

血友病新兴疗法:改善公平获得医疗服务的机会

Lewandowska, Magdalena; Nasr, Sonia; Shapiro, Amy D

Measuring FVIII Activity and Thrombin Generation Simultaneously With a Novel Point of Care Platform (EnzySystem HemA): Qualitative Usability Evaluation

利用新型即时检测平台(EnzySystem HemA)同时测量FVIII活性和凝血酶生成:定性可用性评估

Bavinck, Aernoud; Schols, Saskia E M; Teunissen, Wilfred; Shapiro, Amy; Blijlevens, Nicole M A; Davis, Kyle; van Heerde, Waander

Treatment and Disease Burden in a Cohort of People With Haemophilia Without Inhibitors in the United States

美国一组无抑制因子血友病患者的治疗和疾病负担

Wheeler, Allison P; Cibelli, Emily; Hanson, Gillian; Percier, Cléa; Porstmann, Thomas; Shridhar, Naveen; Shapiro, Amy