Flow-Cytometry Platform for Intracellular Detection of FVIII in Blood Cells: A New Tool to Assess Gene Therapy Efficiency for Hemophilia A
用于检测血细胞内FVIII的流式细胞术平台:评估A型血友病基因治疗效果的新工具
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2019.11.003
Elnaggar, Muhammad; Al-Mohannadi, Anjud; Kizhakayil, Dhanya; Raynaud, Christophe Michel; Al-Mannai, Sharefa; Gentilcore, Giusy; Pavlovski, Igor; Sathappan, Abbirami; Van Panhuys, Nicholas; Borsotti, Chiara; Follenzi, Antonia; Grivel, Jean-Charles; Deola, Sara