Transitioning From Nusinersen to Risdiplam for Spinal Muscular Atrophy in Clinical Practice: A Single-Center Experience
临床实践中脊髓性肌萎缩症治疗从诺西那生过渡到利司他林:单中心经验
期刊:Muscle & Nerve
影响因子:3.1
doi:10.1002/mus.28329
Bekircan-Kurt, Can Ebru; Subramanian, Sharmada; Chagat, Shannon; Mackenzie, Samuel J; Iammarino, Megan; Reash, Natalie; Richardson, Carson; Tsao, Chang-Yong; Noritz, Garey; Gushue, Courtney; Kotha, Kavitha; Paul, Grace; Shell, Richard; Alfano, Lindsay N; Lowes, Linda P; Connolly, Anne M; Waldrop, Megan A