Lysosomal alterations and decreased electrophysiological activity in CLN3 disease patient-derived cortical neurons
CLN3 疾病患者皮质神经元的溶酶体改变和电生理活动降低
期刊:Disease Models & Mechanisms
影响因子:4
doi:10.1242/dmm.049651
Sueanne Chear, Sharn Perry, Richard Wilson, Aidan Bindoff, Jana Talbot, Tyson L Ware, Alexandra Grubman, James C Vickers, Alice Pébay, Jonathan B Ruddle, Anna E King, Alex W Hewitt, Anthony L Cook