Hematopoietic stem cell transplant effectively rescues lymphocyte differentiation and function in DOCK8-deficient patients
造血干细胞移植可有效挽救DOCK8缺陷患者的淋巴细胞分化和功能。
期刊:JCI Insight
影响因子:6.1
doi:10.1172/jci.insight.127527
Pillay, Bethany A; Avery, Danielle T; Smart, Joanne M; Cole, Theresa; Choo, Sharon; Chan, Damien; Gray, Paul E; Frith, Katie; Mitchell, Richard; Phan, Tri Giang; Wong, Melanie; Campbell, Dianne E; Hsu, Peter; Ziegler, John B; Peake, Jane; Alvaro, Frank; Picard, Capucine; Bustamante, Jacinta; Neven, Benedicte; Cant, Andrew J; Uzel, Gulbu; Arkwright, Peter D; Casanova, Jean-Laurent; Su, Helen C; Freeman, Alexandra F; Shah, Nirali; Hickstein, Dennis D; Tangye, Stuart G; Ma, Cindy S