日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

The Influence of Renal or Hepatic Impairment on the Pharmacokinetics of Iclepertin (BI 425809): Results from Two Phase I Open-Label, Non-randomised, Single Dose, Parallel Design Studies

肾功能或肝功能损害对伊克利帕汀(BI 425809)药代动力学的影响:两项 I 期开放标签、非随机、单剂量、平行设计研究的结果

Choi, HeeJae; Madari, Shilpa; Daalman, Elmar; English, Brett A; Halabi, Atef; Hohl, Kathrin; Shatillo, Yury; Weidinger, Nathalie; Desch, Michael

Safety, Pharmacokinetics, and Pharmacodynamics of BI 1595043, a Selective Vanin Inhibitor, in Phase 1 Clinical Trials Involving Healthy Volunteers

BI 1595043(一种选择性Vanin抑制剂)在涉及健康志愿者的I期临床试验中的安全性、药代动力学和药效学

Kukreja, Anjli; Keller, Sascha; Shatillo, Yury; Bauer, Andras; Sharma, Ashish; Wojciekowski, Stephan; Visvanathan, Sudha; Aslanyan, Stella

Automatic Cerebral Hemisphere Segmentation in Rat MRI with Ischemic Lesions via Attention-based Convolutional Neural Networks

基于注意力机制的卷积神经网络在大鼠缺血性病变MRI图像中自动分割大脑半球

Valverde, Juan Miguel; Shatillo, Artem; De Feo, Riccardo; Tohka, Jussi

Heterozygous frameshift variants in HNRNPA2B1 cause early-onset oculopharyngeal muscular dystrophy

HNRNPA2B1基因的杂合移码变异会导致早发性眼咽肌营养不良症

Hong Joo Kim # ,Payam Mohassel # ,Sandra Donkervoort ,Lin Guo ,Kevin O'Donovan ,Maura Coughlin ,Xaviere Lornage ,Nicola Foulds ,Simon R Hammans ,A Reghan Foley ,Charlotte M Fare ,Alice F Ford ,Masashi Ogasawara ,Aki Sato ,Aritoshi Iida ,Pinki Munot ,Gautam Ambegaonkar ,Rahul Phadke ,Dominic G O'Donovan ,Rebecca Buchert ,Mona Grimmel ,Ana Töpf ,Irina T Zaharieva ,Lauren Brady ,Ying Hu ,Thomas E Lloyd ,Andrea Klein ,Maja Steinlin ,Alice Kuster ,Sandra Mercier ,Pascale Marcorelles ,Yann Péréon ,Emmanuelle Fleurence ,Adnan Manzur ,Sarah Ennis ,Rosanna Upstill-Goddard ,Luca Bello ,Cinzia Bertolin ,Elena Pegoraro ,Leonardo Salviati ,Courtney E French ,Andriy Shatillo ,F Lucy Raymond ,Tobias B Haack ,Susana Quijano-Roy ,Johann Böhm ,Isabelle Nelson ,Tanya Stojkovic ,Teresinha Evangelista ,Volker Straub ,Norma B Romero ,Jocelyn Laporte ,Francesco Muntoni ,Ichizo Nishino ,Mark A Tarnopolsky ,James Shorter ,Carsten G Bönnemann ,J Paul Taylor

The Absolute Bioavailability, Absorption, Distribution, Metabolism, and Excretion of BI 425809 Administered as an Oral Dose or an Oral Dose with an Intravenous Microtracer Dose of [(14)C]-BI 425809 in Healthy Males

健康男性口服 BI 425809 或口服联合静脉注射微量示踪剂 [(14)C]-BI 425809 后,其绝对生物利用度、吸收、分布、代谢和排泄情况

Burkard, Ute; Desch, Michael; Shatillo, Yury; Wunderlich, Glen; Mack, Salome Rebecca; Schlecker, Christina; Teitelbaum, Aaron M; Liu, Pingrong; Chan, Tom S

Ethnicity-related DMD Genotype Landscapes in European and Non-European Countries

欧洲和非欧洲国家中与种族相关的DMD基因型分布

Selvatici, Rita; Rossi, Rachele; Fortunato, Fernanda; Trabanelli, Cecilia; Sifi, Yamina; Margutti, Alice; Neri, Marcella; Gualandi, Francesca; Szabò, Lena; Fekete, Balint; Angelova, Lyudmilla; Litvinenko, Ivan; Ivanov, Ivan; Vildan, Yurtsever; Iuhas, Oana Alexandra; Vintan, Mihaela; Burloiu, Carmen; Lacramioara, Butnariu; Visa, Gabriela; Epure, Diana; Rusu, Cristina; Vasile, Daniela; Sandu, Magdalena; Vlodavets, Dmitry; Mager, Monica; Kyriakides, Theodore; Delin, Sanja; Lehman, Ivan; Fureš, Jadranka Sekelj; Bojinova, Veneta; Militaru, Mariela; Guergueltcheva, Velina; Burnyte, Birute; Molnar, Maria Judith; Butoianu, Niculina; Bensemmane, Selma Dounia; Makri-Mokrane, Samira; Herczegfalvi, Agnes; Panzaru, Monica; Emandi, Adela Chirita; Lusakowska, Anna; Potulska-Chromik, Anna; Kostera-Pruszczyk, Anna; Shatillo, Andriy; Khelladi, Djawed Bouchenak; Dendane, Oussama; Fang, Mingyan; Lu, Zhiyuan; Ferlini, Alessandra

RAFF-4, Magnetization Transfer and Diffusion Tensor MRI of Lysophosphatidylcholine Induced Demyelination and Remyelination in Rats

RAFF-4、溶血磷脂酰胆碱诱发的大鼠脱髓鞘和髓鞘再生的磁化转移和扩散张量 MRI

Klara Holikova, Hanne Laakso, Raimo Salo, Artem Shatillo, Antti Nurmi, Martin Bares, Jiri Vanicek, Shalom Michaeli, Silvia Mangia, Alejandra Sierra, Olli Gröhn

Correction to: Eight years after an international workshop on myotonic dystrophy patient registries: case study of a global collaboration for a rare disease

更正:肌强直性营养不良症患者登记国际研讨会八年后:罕见病全球合作案例研究

Wood, Libby; Bassez, Guillaume; Bleyenheuft, Corinne; Campbell, Craig; Cossette, Louise; Jimenez-Moreno, Aura Cecilia; Dai, Yi; Dawkins, Hugh; Díaz-Manera, Jordi; Dogan, Celine; El Sherif, Rasha; Fossati, Barbara; Graham, Caroline; Hilbert, James; Kastreva, Kristinia; Kimura, En; Korngut, Lawrence; Kostera-Pruszczyk, Anna; Lindberg, Christopher; Lindvall, Bjorn; Luebbe, Elizabeth; Lusakowska, Anna; Mazanec, Radim; Meola, Giovani; Orlando, Liannna; Takahashi, Masanori P; Peric, Stojan; Puymirat, Jack; Rakocevic-Stojanovic, Vidosava; Rodrigues, Miriam; Roxburgh, Richard; Schoser, Benedikt; Segovia, Sonia; Shatillo, Andriy; Thiele, Simone; Tournev, Ivailo; van Engelen, Baziel; Vohanka, Stanislav; Lochmüller, Hanns

Eight years after an international workshop on myotonic dystrophy patient registries: case study of a global collaboration for a rare disease

在一次关于强直性肌营养不良症患者登记的国际研讨会召开八年后:一项罕见病全球合作案例研究

Wood, Libby; Bassez, Guillaume; Bleyenheuft, Corinne; Campbell, Craig; Cossette, Louise; Jimenez-Moreno, Aura Cecilia; Dai, Yi; Dawkins, Hugh; Manera, Jorge Alberto Diaz; Dogan, Celine; El Sherif, Rasha; Fossati, Barbara; Graham, Caroline; Hilbert, James; Kastreva, Kristinia; Kimura, En; Korngut, Lawrence; Kostera-Pruszczyk, Anna; Lindberg, Christopher; Lindvall, Bjorn; Luebbe, Elizabeth; Lusakowska, Anna; Mazanec, Radim; Meola, Giovani; Orlando, Liannna; Takahashi, Masanori P; Peric, Stojan; Puymirat, Jack; Rakocevic-Stojanovic, Vidosava; Rodrigues, Miriam; Roxburgh, Richard; Schoser, Benedikt; Segovia, Sonia; Shatillo, Andriy; Thiele, Simone; Tournev, Ivailo; van Engelen, Baziel; Vohanka, Stanislav; Lochmüller, Hanns

Inaugural Charles River World Congress on Animal Models in Drug Discovery and Development

首届查尔斯河药物发现与开发动物模型世界大会

Kesireddy, Venu; Kasper, F Kurtis; Berzofsky, Jay A; Koch, Lauren Gerard; Britton, Steven L; Chen, Shaochen; Zhu, Wei; Ma, Xuanyi; Comuzzie, Anthony G; Devy-Dimanche, Laetitia; Feaver, Ryan; Grimm, Jan; Hock, Christoph; Nitsch, Roger M; Hoying, James B; Lusis, Aldons J; Marincola, Francesco; Samayoa, Josue; Turan, Tolga; Pearce, David A; Nurmi, Antti; Huhtala, Tuulia; Shatillo, Artem; Puoliväli, Jukka; Heikkinen, Taneli; Bragge, Timo; Lehtimäki, Kimmo; Sanyal, Arun J; Strange, Kevin; Taylor, D Lansing; Miedel, Mark; Jia, Shanhang; Soto-Guterriez, Alex; Stern, Andrew; Gough, Albert