日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

AAV-delivered engineered suppressor tRNA rescues visual function in mice with an inherited retinal disease.

利用 AAV 递送的工程化抑制 tRNA 可挽救患有遗传性视网膜疾病的小鼠的视觉功能。

Ren Chengda, Song Li, Hu Ming, Jin Xiu, Liang Licong, Liu Fanfei, Su Jing, Fu Jiamei, Yang Yiliu, Liu Man, Xu Qiuxia, Wu Xiaoyi, Luo Min, Ye Qin, Li Qiqi, An Yifang, Li Manjun, She Kaiqin, Wei Yuquan, Lu Fang, Yang Yang

Retinal Pigment Epithelium-Targeting Gene Therapy Corrects Ocular Symptoms in Mouse and Rat Models of Oculocutaneous Albinism Type I

视网膜色素上皮靶向基因疗法可纠正小鼠和大鼠I型眼皮肤白化病模型中的眼部症状

Song, Li; Ren, Chengda; Luo, Min; Su, Jing; Jin, Xiu; Fu, Jiamei; Xu, Qiuxia; Wu, Xiaoyi; Liu, Fanfei; Ye, Qin; Hu, Ming; Liu, Man; Li, Qiqi; An, Yifang; Li, Manjun; Wang, Qingnan; She, Kaiqin; Lu, Fang; Yang, Yang

Multimodal optical imaging of iris flocculi in three consecutive generations: a case report

连续三代虹膜绒毛的多模态光学成像:病例报告

Jiang, Anna; Liang, Licong; She, Kaiqin; Lu, Fang

Dual-AAV split prime editor corrects the mutation and phenotype in mice with inherited retinal degeneration.

双 AAV 分裂启动编辑器可纠正患有遗传性视网膜变性的小鼠的突变和表型

She Kaiqin, Liu Yi, Zhao Qinyu, Jin Xiu, Yang Yiliu, Su Jing, Li Ruiting, Song Li, Xiao Jianlu, Yao Shaohua, Lu Fang, Wei Yuquan, Yang Yang

In vivo adenine base editing corrects newborn murine model of Hurler syndrome.

体内腺嘌呤碱基编辑可纠正新生小鼠赫勒氏综合征模型

Su Jing, Jin Xiu, She Kaiqin, Liu Yi, Song Li, Zhao Qinyu, Xiao Jianlu, Li Ruiting, Deng Hongxin, Lu Fang, Yang Yang

Blocking Th2 Signaling Pathway Alleviates the Clinical Symptoms and Inflammation in Allergic Conjunctivitis

阻断Th2信号通路可缓解过敏性结膜炎的临床症状和炎症

Tao, Zhiyan; Liu, Wei; Chen, Qin; Zhang, Libo; She, Kaiqin; Zhao, Guoqing; Liang, Licong; Chen, Xuhong; Yang, Yiliu; Song, Qin; Lu, Fang

Visual Acuity-Related Outer Retinal Structural Parameters on Swept Source Optical Coherence Tomography and Angiography in XLRS Patients and Carriers

X射线视网膜病变患者和携带者通过扫频源光学相干断层扫描和血管造影术检测与视力相关的外层视网膜结构参数

Tao, Zhiyan; Bu, Shaochong; Liang, Licong; Yang, Yiliu; She, Kaiqin; Lu, Fang

CRISPR/Cas systems usher in a new era of disease treatment and diagnosis

CRISPR/Cas系统开启了疾病治疗和诊断的新时代

Li, Ruiting; Wang, Qin; She, Kaiqin; Lu, Fang; Yang, Yang

Clinical and Echographic Features of Morning Glory Disc Anomaly in Children: A Retrospective Study of 249 Chinese Patients

儿童牵牛花状椎间盘异常的临床和超声特征:一项对249例中国患者的回顾性研究

Zou, Yihua; She, Kaiqin; Hu, Yiqian; Ren, Jianing; Fei, Ping; Xu, Yu; Peng, Jie; Zhao, Peiquan

A case of anterior persistent hyperplastic primary vitreous associated with morning glory disc anomaly and retinopathy of prematurity like retinopathy in a term-born child

一例足月儿前部持续性增生性原发性玻璃体伴牵牛花状视盘异常和早产儿视网膜病变样视网膜病变的病例报告

Zhang, Hao; She, Kaiqin; Lu, Fang