Genome editing of HBG1 and HBG2 to induce fetal hemoglobin
HBG1 和 HBG2 基因组编辑诱导胎儿血红蛋白
期刊:Blood Advances
影响因子:7.4
doi:10.1182/bloodadvances.2019000820
Jean-Yves Métais, Phillip A Doerfler, Thiyagaraj Mayuranathan, Daniel E Bauer, Stephanie C Fowler, Matthew M Hsieh, Varun Katta, Sagar Keriwala, Cicera R Lazzarotto, Kevin Luk, Michael D Neel, S Scott Perry, Samuel T Peters, Shaina N Porter, Byoung Y Ryu, Akshay Sharma, Devlin Shea, John F Tisdale,