Defining Satisfactory Methods of Treatment in Rare Diseases When Evaluating Significant Benefit-The EU Regulator's Perspective
在评估显著疗效时,如何界定罕见病治疗的满意方法——欧盟监管机构的视角
期刊:Frontiers in Medicine
影响因子:3
doi:10.3389/fmed.2021.744625
Sheean, Maria E; Naumann-Winter, Frauke; Capovilla, Giuseppe; Kalland, Maria Elisabeth; Malikova, Eva; Mariz, Segundo; Matusevicius, Darius; Nistico, Robert; Schwarzer-Daum, Brigitte; Tsigkos, Stelios; Tzogani, Kyriaki; Larsson, Kristina; Magrelli, Armando; Stoyanova-Beninska, Violeta