日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Intrathecal onasemnogene abeparvovec in treatment-naive patients with spinal muscular atrophy: a phase 3, randomized controlled trial

鞘内注射onasemnogene abeparvovec治疗初治脊髓性肌萎缩症患者:一项3期随机对照试验

Proud, Crystal M; Vũ, Dũng Chí; Wilmshurst, Jo M; Sanmaneechai, Oranee; Gulati, Sheffali; Xiong, Hui; Moreno, Hugo C; Tay, Stacey Kiat Hong; Thong, Meow-Keong; Born, Alfred Peter; Banzzatto Ortega, Adriana; Jong, Yuh-Jyh; Al-Muhaizea, Mohammad A; Lee, Anna W; Visootsak, Jeannie; Tauscher-Wisniewski, Sitra; Alecu, Iulian; Parlikar, Rutvick; Finkel, Richard S

Confirmatory long-term efficacy and safety results of ataluren in patients with nmDMD from Study 041, an international, randomized, double-blind, placebo-controlled, Phase III trial

来自 041 研究的确认性长期疗效和安全性结果,该研究是一项国际性、随机、双盲、安慰剂对照的 III 期试验,旨在评估阿塔卢伦治疗非转移性杜氏肌营养不良症 (nmDMD) 患者的疗效和安全性。

Vlodavets, Dmitry; Wu, Shiwen; Kostera-Pruszczyk, Anna; Chae, Jong-Hee; Gulati, Sheffali; Shin, Jin-Hong; Lorentzos, Michelle; Cairns, Anita; Jong, Yuh-Jyh; Komaki, Hirofumi; Statland, Jeffrey; de Queiroz Campos Araujo, Alexandra Prufer; Gurgel-Giannetti, Juliana; Takeshima, Yasuhiro; Escobar Cedillo, Rosa E; Karachunski, Peter; Haginoya, Kazuhiro; Penematsa, Vinay; Chou, Connie; Williams, Paula; Werner, Christian; McDonald, Craig M

Scoping review of evidence-based practice guidelines for the evaluation and care of young children with developmental disabilities in LMIC settings: evidence for action

低收入和中等收入国家发育障碍幼儿评估和护理循证实践指南的范围界定综述:行动的证据

Magai, Dorcas N; Berman, Brad D; Mutua, Agnes M; Smythe, Tracey; Olusanya, Bolajoko O; Gulati, Sheffali; Mwesige, Angelina Kakooza; Blaikie, Andrew; Lusobya, Rebecca Claire; Coghill, David; Gladstone, Melissa

The pattern of visual impairment in the spectrum of hypoxic ischemic encephalopathy

缺氧缺血性脑病谱系中视觉障碍的模式

Phuljhele, Swati; Balasubramaniam, Niranjana; Saluja, Gunjan; Saxena, Rohit; Sharma, Pradeep; Kumar, Pavan; Kusiyait, Sanjay; Gulati, Sheffali

Agreement Between a Questionnaire-Based Tool and Experienced Pediatric Neurologists in Classifying Seizure Types in Children with Epilepsy

基于问卷调查的工具与经验丰富的儿科神经科医生在对儿童癫痫发作类型进行分类方面的一致性

Choudhary, Puneet Kumar; Tiwari, Richa; Kaur, Prabhjot; Bansal, Shivam; Puri, Gopal; Srividya, P; Pasani, Satwik; Kamila, Gautam; Jauhari, Prashant; Chakrabarty, Biswaroop; Lodha, Rakesh; Pandey, Ravindra Mohan; Paul, Vinod Kumar; Gulati, Sheffali

Air Pollution Impact on Pregnancy and Early Childhood Development (APiPED) in India: Protocol for a Cohort Study

印度空气污染对孕期和幼儿早期发育的影响(APiPED):队列研究方案

Salve, Harshal Ramesh; Dey, Sagnik; Arora, Yashika; Kapoor, Surbhi; Ghosh, Santu; Kumar, Rakesh; Gulati, Sheffali; Sagar, Rajesh; Datta, Sudip Kumar; Krishnan, Anand

Using mobile health technology to assess childhood autism in low-resource community settings in India: An innovation to address the detection gap

利用移动健康技术评估印度资源匮乏社区儿童自闭症:一项旨在弥合检测差距的创新举措

Dubey, Indu; Bishain, Rahul; Dasgupta, Jayashree; Bhavnani, Supriya; Belmonte, Matthew K; Gliga, Teodora; Mukherjee, Debarati; Lockwood Estrin, Georgia; Johnson, Mark H; Chandran, Sharat; Patel, Vikram; Gulati, Sheffali; Divan, Gauri; Chakrabarti, Bhismadev

Locked down-locked in: experiences of families of young children with autism spectrum disorders in Delhi, India

封锁——被困:印度德里自闭症谱系障碍儿童家庭的经历

Kaur, Abhipreet; Lall, Gitanjali; Abhilashi, Minal; Naithani, Lavangi; Verma, Mamta; Roy, Reetabrata; Juneja, Monica; Gulati, Sheffali; Taylor, Carol; Leadbitter, Kathy; Patel, Vikram; Green, Jonathan; Divan, Gauri

Scalable Transdiagnostic Early Assessment of Mental Health (STREAM): a study protocol

可扩展的跨诊断早期心理健康评估(STREAM):一项研究方案

Williams, Elin H; Thompson, Nicholas M; McCray, Gareth; Crespo-Llado, Maria M; Bhavnani, Supriya; Gajria, Diksha; Mukherjee, Debarati; Del Bianco, Teresa; Lockwood-Estrin, Georgia; Mason, Luke; Ngoma, Vukiwe; Namathanga, Chisomo; Nkhata, Richard; Bennie, Allan; Ranjan, Alok; Kawelama, Ulemu; Midha, Naina; Singh, Anindita; Mpakiza, Innocent; Gautam, Akshat; Gulati, Sheffali; Johnson, Mark H; Lancaster, Gillian; Belmonte, Matthew K; Jones, Emily; Patel, Vikram; Chandran, Sharat; Mbale, Emmie; Divan, Gauri; Gladstone, Melissa; Chakrabarti, Bhismadev

Advancements in Dravet Syndrome Therapeutics: A Comprehensive Look at Present and Future Treatment Horizons: A Focused Review

Dravet综合征治疗进展:对当前和未来治疗前景的全面展望:重点综述

Mahesan, Aakash; Kamila, Gautam; Gulati, Sheffali