日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Genetically corrected RAG2-SCID human hematopoietic stem cells restore V(D)J-recombinase and rescue lymphoid deficiency

基因校正的RAG2-SCID人类造血干细胞可恢复V(D)J重组酶并挽救淋巴细胞缺陷

Pavel-Dinu, Mara; Gardner, Cameron L; Nakauchi, Yusuke; Kawai, Tomoki; Delmonte, Ottavia M; Palterer, Boaz; Bosticardo, Marita; Pala, Francesca; Viel, Sebastien; Malech, Harry L; Ghanim, Hana Y; Bode, Nicole M; Kurgan, Gavin L; Detweiler, Angela M; Vakulskas, Christopher A; Neff, Norma F; Sheikali, Adam; Menezes, Sherah T; Chrobok, Jade; Hernández González, Elaine M; Majeti, Ravindra; Notarangelo, Luigi D; Porteus, Matthew H

Jordan's Pandemic Influenza Preparedness (PIP): A Reflection on COVID-19 Response

约旦应对流感大流行的准备工作(PIP):对新冠肺炎疫情应对的反思

Kheirallah, Khalid A; Al-Nusair, Mohammed; Aljabeiti, Shahed; Sheikali, Nadir; Alzoubi, Abdallah; Alsulaiman, Jomana W; Al-Mistarehi, Abdel-Hameed; Alzoubi, Hamed; Bani Mousa, Ayman Ahmad; Allouh, Mohammed Z

Improved Genome Editing through Inhibition of FANCM and Members of the BTR Dissolvase Complex

通过抑制 FANCM 和 BTR 溶解酶复合物成员来改善基因组编辑

Gustavo de Alencastro, Francesco Puzzo, Mara Pavel-Dinu, Feijie Zhang, Sirika Pillay, Karim Majzoub, Matthew Tiffany, Hagoon Jang, Adam Sheikali, M Kyle Cromer, Ruhikanta Meetei, Jan E Carette, Matthew H Porteus, Katja Pekrun, Mark A Kay

Prioritizing zoonotic diseases utilizing the One Health approach: Jordan's experience

利用“同一健康”理念优先应对人畜共患病:约旦的经验

Kheirallah, Khalid A; Al-Mistarehi, Abdel-Hameed; Alsawalha, Lora; Hijazeen, Zaidoun; Mahrous, Heba; Sheikali, Sami; Al-Ramini, Salam; Maayeh, Mohammad; Dodeen, Rachel; Farajeh, Mahmoud; Masadeh, Nezar; Alemam, Amer; Alsulaiman, Jomana; Samhouri, Dalia

Engineering monocyte/macrophage-specific glucocerebrosidase expression in human hematopoietic stem cells using genome editing

利用基因组编辑技术在人类造血干细胞中构建单核细胞/巨噬细胞特异性葡糖脑苷脂酶表达。

Samantha G Scharenberg # ,Edina Poletto # ,Katherine L Lucot ,Pasqualina Colella ,Adam Sheikali ,Thomas J Montine ,Matthew H Porteus ,Natalia Gomez-Ospina

CRISPR-based gene editing enables FOXP3 gene repair in IPEX patient cells

基于 CRISPR 的基因编辑可修复 IPEX 患者细胞中的 FOXP3 基因

M Goodwin, E Lee, U Lakshmanan, S Shipp, L Froessl, F Barzaghi, L Passerini, M Narula, A Sheikali, C M Lee, G Bao, C S Bauer, H K Miller, M Garcia-Lloret, M J Butte, A Bertaina, A Shah, M Pavel-Dinu, A Hendel, M Porteus, M G Roncarolo, R Bacchetta