日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Outcomes following matched sibling donor transplantation for severe combined immunodeficiency: a report from the PIDTC

同胞相合供体移植治疗重症联合免疫缺陷的疗效:来自PIDTC的报告

Rayes, Ahmad; Logan, Brent R; Liu, Xuerong; Dara, Jasmeen; Buckley, Rebecca H; Oved, Joseph H; Kapoor, Neena; Kapadia, Malika; Chandra, Sharat; Martinez, Caridad A; Bunin, Nancy J; Chandrakasan, Shanmuganathan; Chen, Karin; Bednarski, Jeffrey J; Haines, Hilary L; Eissa, Hesham; Talano, Julie-An M; Keller, Michael D; Ebens, Christen L; Chaudhury, Sonali; Shereck, Evan B; Aquino, Victor M; Knutsen, Alan P; Alexander, Jessie L; Gillio, Alfred P; Chellapandian, Deepakbabu; Shah, Ami J; Miller, Holly K; Vander Lugt, Mark T; Seroogy, Christine M; Dorsey, Morna J; Mousallem, Talal; Parrott, Roberta E; O'Reilly, Richard J; Aguayo-Hiraldo, Paibel I; Prockop, Susan E; Dávila Saldaña, Blachy J; Thakar, Monica S; Burroughs, Lauri M; Torgerson, Troy R; Leiding, Jennifer W; Marsh, Rebecca A; Griffith, Linda M; Pulsipher, Michael A; Kohn, Donald B; Notarangelo, Luigi; Cowan, Morton J; Puck, Jennifer M; Cuvelier, Geoffrey D E; Heimall, Jennifer; Haddad, Elie; Pai, Sung-Yun; Dvorak, Christopher C

Hematopoietic cell transplantation for Wiskott-Aldrich syndrome: a PIDTC report

造血干细胞移植治疗威斯科特-奥尔德里奇综合征:PIDTC报告

Alexander, Jessie L; Dávila Saldaña, Blachy J; Brazauskas, Ruta; Dammalapati, Sravya Gethika; Griffith, Linda M; Shah, Ami J; Shimano, Kristin A; Ochs, Hans D; Bleesing, Jack J; Ebens, Christen L; Kapadia, Malika; Bauchat, Andrea; Kapoor, Neena; Oved, Joseph H; Eissa, Hesham; Lust, Hannah; Keller, Michael D; Haines, Hilary; Chandrakasan, Shanmuganathan; Talano, Julie-An; Rayes, Ahmad; Madden, Lisa; Shereck, Evan; Miller, Holly K; Satter, Lisa Forbes; Martinez, Caridad; Rozmus, Jacob; Bednarski, Jeffrey J; Yu, Lolie C; Chellapandian, Deepakbabu; Aquino, Victor M; Knutsen, Alan; Chong, Hey; Chopek, Ashley; Gillio, Alfred P; Joshi, Avni; Rangarajan, Hemalatha; Moore, Theodore B; Andolina, Jeffrey R; DeSantes, Kenneth B; Vander Lugt, Mark; Prockop, Susan E; Shyr, David C; Sullivan, Kathleen E; Parikh, Suhag; Weinacht, Katja G; Torgerson, Troy R; Marsh, Rebecca; Dvorak, Christopher C; Chan, Alice Y; Haddad, Elie; Heimall, Jennifer R; Pulsipher, Michael A; Leiding, Jennifer W; Kohn, Donald B; Puck, Jennifer M; Notarangelo, Luigi D; Rawlings, David J; Cowan, Morton J; Petrovic, Aleksandra; Pai, Sung-Yun; Burroughs, Lauri M

"Tough Things You're Going to Have to Go Through": Dyadic Interview Study Including the Perspectives and Needs of Patients and Their Caregivers Post-Hematopoietic Cell Transplant

“你将要经历的艰难时刻”:一项关于造血干细胞移植后患者及其照护者观点和需求的双人访谈研究

Johnson, Amanda; Smeallie, Eleanor; Roslin, Chloe; Rozwadowski, Michelle; Shereck, Evan; Choi, Sung Won

A Mobile Health Intervention in Caregivers of Patients Undergoing Hematopoietic Cell Transplantation: A Randomized Controlled Trial to Examine Health-Related Quality of Life

一项针对接受造血干细胞移植患者照护者的移动健康干预:一项旨在检验健康相关生活质量的随机对照试验

Cao, Xiao; Rozwadowski, Michelle; Braun, Thomas M; Carlozzi, Noelle E; Hassett, Afton L; Johnson, Amanda K; Shereck, Evan; Hanauer, David A; Choi, Sung Won

Posttransplantation late complications increase over time for patients with SCID: A Primary Immune Deficiency Treatment Consortium (PIDTC) landmark study

移植后晚期并发症在重症联合免疫缺陷病(SCID)患者中随时间推移而增加:一项原发性免疫缺陷治疗联盟(PIDTC)里程碑式研究

Eissa, Hesham; Thakar, Monica S; Shah, Ami J; Logan, Brent R; Griffith, Linda M; Dong, Huaying; Parrott, Roberta E; O'Reilly, Richard J; Dara, Jasmeen; Kapoor, Neena; Forbes Satter, Lisa; Chandra, Sharat; Kapadia, Malika; Chandrakasan, Shanmuganathan; Knutsen, Alan; Jyonouchi, Soma C; Molinari, Lyndsay; Rayes, Ahmad; Ebens, Christen L; Teira, Pierre; Dávila Saldaña, Blachy J; Burroughs, Lauri M; Chaudhury, Sonali; Chellapandian, Deepak; Gillio, Alfred P; Goldman, Fredrick; Malech, Harry L; DeSantes, Kenneth; Cuvelier, Geoff D E; Rozmus, Jacob; Quinones, Ralph; Yu, Lolie C; Broglie, Larisa; Aquino, Victor; Shereck, Evan; Moore, Theodore B; Vander Lugt, Mark T; Mousallem, Talal I; Oved, Joeseph H; Dorsey, Morna; Abdel-Azim, Hisham; Martinez, Caridad; Bleesing, Jacob H; Prockop, Susan; Kohn, Donald B; Bednarski, Jeffrey J; Leiding, Jennifer; Marsh, Rebecca A; Torgerson, Troy; Notarangelo, Luigi D; Pai, Sung-Yun; Pulsipher, Michael A; Puck, Jennifer M; Dvorak, Christopher C; Haddad, Elie; Buckley, Rebecca H; Cowan, Morton J; Heimall, Jennifer

Relevance of lymphocyte proliferation to PHA in severe combined immunodeficiency (SCID) and T cell lymphopenia

淋巴细胞增殖与严重联合免疫缺陷(SCID)和T细胞淋巴细胞减少症中植物血凝素(PHA)的相关性

Abraham, Roshini S; Basu, Amrita; Heimall, Jennifer R; Dunn, Elizabeth; Yip, Alison; Kapadia, Malika; Kapoor, Neena; Satter, Lisa Forbes; Buckley, Rebecca; O'Reilly, Richard; Cuvelier, Geoffrey D E; Chandra, Sharat; Bednarski, Jeffrey; Chaudhury, Sonali; Moore, Theodore B; Haines, Hilary; Dávila Saldaña, Blachy J; Chellapandian, Deepakbabu; Rayes, Ahmad; Chen, Karin; Caywood, Emi; Chandrakasan, Shanmuganathan; Lugt, Mark Thomas Vander; Ebens, Christen; Teira, Pierre; Shereck, Evan; Miller, Holly; Aquino, Victor; Eissa, Hesham; Yu, Lolie C; Gillio, Alfred; Madden, Lisa; Knutsen, Alan; Shah, Ami J; DeSantes, Kenneth; Barnum, Jessie; Broglie, Larisa; Joshi, Avni Y; Kleiner, Gary; Dara, Jasmeen; Prockop, Susan; Martinez, Caridad; Mousallem, Talal; Oved, Joseph; Burroughs, Lauri; Marsh, Rebecca; Torgerson, Troy R; Leiding, Jennifer W; Pai, Sung Yun; Kohn, Donald B; Pulsipher, Michael A; Griffith, Linda M; Notarangelo, Luigi D; Cowan, Morton J; Puck, Jennifer; Dvorak, Christopher C; Haddad, Elie

Measuring the effect of newborn screening on survival after haematopoietic cell transplantation for severe combined immunodeficiency: a 36-year longitudinal study from the Primary Immune Deficiency Treatment Consortium

衡量新生儿筛查对重症联合免疫缺陷造血干细胞移植后生存率的影响:来自原发性免疫缺陷治疗联盟的一项为期36年的纵向研究

Thakar, Monica S; Logan, Brent R; Puck, Jennifer M; Dunn, Elizabeth A; Buckley, Rebecca H; Cowan, Morton J; O'Reilly, Richard J; Kapoor, Neena; Satter, Lisa Forbes; Pai, Sung-Yun; Heimall, Jennifer; Chandra, Sharat; Ebens, Christen L; Chellapandian, Deepak; Williams, Olatundun; Burroughs, Lauri M; Saldana, Blachy Davila; Rayes, Ahmad; Madden, Lisa M; Chandrakasan, Shanmuganathan; Bednarski, Jeffrey J 2nd; DeSantes, Kenneth B; Cuvelier, Geoffrey D E; Teira, Pierre; Gillio, Alfred P; Eissa, Hesham; Knutsen, Alan P; Goldman, Frederick D; Aquino, Victor M; Shereck, Evan B; Moore, Theodore B; Caywood, Emi H; Lugt, Mark T Vander; Rozmus, Jacob; Broglie, Larisa; Yu, Lolie C; Shah, Ami J; Andolina, Jeffrey R; Liu, Xuerong; Parrott, Roberta E; Dara, Jasmeen; Prockop, Susan; Martinez, Caridad A; Kapadia, Malika; Jyonouchi, Soma C; Sullivan, Kathleen E; Bleesing, Jack J; Chaudhury, Sonali; Petrovic, Aleksandra; Keller, Michael D; Quigg, Troy C; Parikh, Suhag; Shenoy, Shalini; Seroogy, Christine; Rubin, Tamar; Decaluwe, Hélène; Routes, John M; Torgerson, Troy R; Leiding, Jennifer W; Pulsipher, Michael A; Kohn, Donald B; Griffith, Linda M; Haddad, Elie; Dvorak, Christopher C; Notarangelo, Luigi D

The diagnosis of severe combined immunodeficiency: Implementation of the PIDTC 2022 Definitions

重症联合免疫缺陷的诊断:PIDTC 2022 定义的实施

Dvorak, Christopher C; Haddad, Elie; Heimall, Jennifer; Dunn, Elizabeth; Cowan, Morton J; Pai, Sung-Yun; Kapoor, Neena; Satter, Lisa Forbes; Buckley, Rebecca H; O'Reilly, Richard J; Chandra, Sharat; Bednarski, Jeffrey J; Williams, Olatundun; Rayes, Ahmad; Moore, Theodore B; Ebens, Christen L; Davila Saldana, Blachy J; Petrovic, Aleksandra; Chellapandian, Deepak; Cuvelier, Geoffrey D E; Vander Lugt, Mark T; Caywood, Emi H; Chandrakasan, Shanmuganathan; Eissa, Hesham; Goldman, Frederick D; Shereck, Evan; Aquino, Victor M; Desantes, Kenneth B; Madden, Lisa M; Miller, Holly K; Yu, Lolie; Broglie, Larisa; Gillio, Alfred; Shah, Ami J; Knutsen, Alan P; Andolina, Jeffrey P; Joshi, Avni Y; Szabolcs, Paul; Kapadia, Malika; Martinez, Caridad A; Parrot, Roberta E; Sullivan, Kathleen E; Prockop, Susan E; Abraham, Roshini S; Thakar, Monica S; Leiding, Jennifer W; Kohn, Donald B; Pulsipher, Michael A; Griffith, Linda M; Notarangelo, Luigi D; Puck, Jennifer M

Success and Satisfaction with Virtual Hematology Curriculum Implemented in Response to COVID-19

为应对新冠疫情而实施的虚拟血液学课程的成功与满意度

Wang, X; Qin, T J; Xu, Z F; Qu, S Q; Li, B; Pan, L J; Gao, Q Y; Jiao, M; Zhong, Y; Jiang, B H; Liu, L L; Zhao, J Y; Xie, W J; Xiao, Z J; Gunesch, Ali Noel; McClellan, Kristen; Meyers, Gabrielle; Shereck, Evan

Excellent outcomes following hematopoietic cell transplantation for Wiskott-Aldrich syndrome: a PIDTC report

造血干细胞移植治疗威斯科特-奥尔德里奇综合征取得优异疗效:PIDTC报告

Burroughs, Lauri M; Petrovic, Aleksandra; Brazauskas, Ruta; Liu, Xuerong; Griffith, Linda M; Ochs, Hans D; Bleesing, Jack J; Edwards, Stephanie; Dvorak, Christopher C; Chaudhury, Sonali; Prockop, Susan E; Quinones, Ralph; Goldman, Frederick D; Quigg, Troy C; Chandrakasan, Shanmuganathan; Smith, Angela R; Parikh, Suhag; Dávila Saldaña, Blachy J; Thakar, Monica S; Phelan, Rachel; Shenoy, Shalini; Forbes, Lisa R; Martinez, Caridad; Chellapandian, Deepak; Shereck, Evan; Miller, Holly K; Kapoor, Neena; Barnum, Jessie L; Chong, Hey; Shyr, David C; Chen, Karin; Abu-Arja, Rolla; Shah, Ami J; Weinacht, Katja G; Moore, Theodore B; Joshi, Avni; DeSantes, Kenneth B; Gillio, Alfred P; Cuvelier, Geoffrey D E; Keller, Michael D; Rozmus, Jacob; Torgerson, Troy; Pulsipher, Michael A; Haddad, Elie; Sullivan, Kathleen E; Logan, Brent R; Kohn, Donald B; Puck, Jennifer M; Notarangelo, Luigi D; Pai, Sung-Yun; Rawlings, David J; Cowan, Morton J