Highly efficient neuronal gene knockout in vivo by CRISPR-Cas9 via neonatal intracerebroventricular injection of AAV in mice
通过在小鼠新生儿脑室内注射 AAV 实现 CRISPR-Cas9 体内高效神经元基因敲除
期刊:Gene Therapy
影响因子:4.6
doi:10.1038/s41434-021-00224-2
Sam Hana, Michael Peterson, Helen McLaughlin, Eric Marshall, Attila J Fabian, Olivia McKissick, Kathryn Koszka, Galina Marsh, Michael Craft, Shanqin Xu, Alexander Sorets, Tess Torregrosa, Chao Sun, Chris E Henderson, Shih-Ching Lo