Potent and durable gene modulation in heart and muscle with chemically defined lipophilic siRNAs
利用化学成分明确的亲脂性siRNA在心脏和肌肉中实现高效持久的基因调控
期刊:Nucleic Acids Research
影响因子:13.1
doi:10.1093/nar/gkaf1374
Fakih, Hassan H; Lochmann, Clemens; Gagnon, Rosemary; Summers, Ashley; Caiazzi, Jillian; Buchwald, Julianna E; Tang, Qi; Maru, Bruktawit; Hildebrand, Samuel R; Abideen, Mohammad Zain U I; Furgal, Raymond C; Gross, Katherine Y; Yang, Yeon-Suk; Cooper, David; Monopoli, Kathryn R; Echeverria, Dimas; Shim, Jae-Hyuck; Yamada, Ken; Alterman, Julia F; Khvorova, Anastasia