CRISPR-Cas9 Screens Identify the RNA Helicase DDX3X as a Repressor of C9ORF72 (GGGGCC)n Repeat-Associated Non-AUG Translation
CRISPR-Cas9 筛选鉴定出 RNA 解旋酶 DDX3X 是 C9ORF72 (GGGGCC)n 重复相关非 AUG 翻译的抑制因子
期刊:Neuron
影响因子:14.7
doi:10.1016/j.neuron.2019.09.003
Weiwei Cheng, Shaopeng Wang, Zhe Zhang, David W Morgens, Lindsey R Hayes, Soojin Lee, Bede Portz, Yongzhi Xie, Baotram V Nguyen, Michael S Haney, Shirui Yan, Daoyuan Dong, Alyssa N Coyne, Junhua Yang, Fengfan Xian, Don W Cleveland, Zhaozhu Qiu, Jeffrey D Rothstein, James Shorter, Fen-Biao Gao, Micha