Enhanced transgene expression from single-stranded AAV vectors in human cells in vitro and in murine hepatocytes in vivo.
单链 AAV 载体在体外人类细胞和体内小鼠肝细胞中增强转基因表达
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.1
doi:10.1016/j.omtn.2024.102196
Lu Yuan, Ling Chen, Shoti Jakob, Yang Hua, Nath Aneesha, Keeler Geoffrey D, Qing Keyun, Srivastava Arun
