Restoring neuronal chloride homeostasis with anti-NKCC1 gene therapy rescues cognitive deficits in a mouse model of Down syndrome
利用抗 NKCC1 基因疗法恢复神经元氯离子稳态可挽救唐氏综合症小鼠模型的认知缺陷
期刊:Molecular Therapy
影响因子:12.1
doi:10.1016/j.ymthe.2021.05.023
Martina Parrini, Shovan Naskar, Micol Alberti, Ilaria Colombi, Giovanni Morelli, Anna Rocchi, Marina Nanni, Federica Piccardi, Severine Charles, Giuseppe Ronzitti, Federico Mingozzi, Andrea Contestabile, Laura Cancedda