Nanoparticle delivery of CRISPR into the brain rescues a mouse model of fragile X syndrome from exaggerated repetitive behaviours
将 CRISPR 纳米颗粒递送至大脑，拯救了患有脆性 X 综合征的小鼠模型，使其摆脱夸张的重复行为
期刊:Nature Biomedical Engineering
影响因子:26.8
doi:10.1038/s41551-018-0252-8
Bumwhee Lee, Kunwoo Lee, Shree Panda, Rodrigo Gonzales-Rojas, Anthony Chong, Vladislav Bugay, Hyo Min Park, Robert Brenner, Niren Murthy, Hye Young Lee
