MON-749 Long-Term in Vivo Expression of Tissue Nonspecific Alkaline Phosphatase by Ex Vivo Gene Edited B Cells as a Potential Treatment of Hypophosphatasia
MON-749:体外基因编辑B细胞在体内长期表达组织非特异性碱性磷酸酶,作为低磷酸血症的潜在治疗方法
期刊:Evidence-Based Complementary and Alternative Medicine
影响因子:
doi:10.1155/2018/4365739
Gong, Benjiao; Kao, Yanlei; Zhang, Chenglin; Sun, Fudong; Zhao, Huishan; Pierog, Piotr; Brophy, Megan; Wong, Wesley; Zhang, Xuqing; Li, Lily; Hickey, Jennifer; Lundberg, Amy; Bainter, Wayne; Bullock, Caroline; Keegan, Sean; Bedard-Shurtleff, Suzanne; Mullen, Timothy; Edelstein, Jasmine; Bhawsar, Shivani; Adekanye, Glory; Liberzon, Ella; Singh, Swati; Musial-Siwek, Monika; Hohmann, Anja; Arlauckas, Sean; Lazorchak, Adam; Liu, Hanlan; Morgan, Richard; Pierog, Piotr; Brophy, Megan; Wong, Wesley; Zhang, Xuqing; Li, Lily; Hickey, Jennifer; Lundberg, Amy; Bainter, Wayne; Bullock, Caroline; Keegan, Sean; Bedard-Shurtleff, Suzanne; Mullen, Timothy; Edelstein, Jasmine; Bhawsar, Shivani; Adekanye, Glory; Liberzon, Ella; Singh, Swati; Musial-Siwek, Monika; Hohmann, Anja; Arlauckas, Sean; Lazorchak, Adam; Liu, Hanlan; Morgan, Richard