日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Targeting DNA-LNPs to Endothelial Cells Improves Expression Magnitude, Duration, and Specificity

将DNA-LNP靶向内皮细胞可提高表达强度、持续时间和特异性

Marzolini, Nicolas; Brysgel, Taylor V; Rahman, Ryan J; Essien, Eno-Obong; Nwe, Saw Y; Wu, Jichuan; Majumder, Aparajeeta; Patel, Manthan N; Tiwari, Sachchidanand; Espy, Carolann L; Dong, Fengyi; Santos-De León, Sabrina A; Shah, Anit; Shuvaev, Vladimir V; Hood, Elizabeth D; Chase, Liam S; Weissman, Drew; Katzen, Jeremy B; Frank, David B; Bennett, Mariko L; Marcos-Contreras, Oscar A; Myerson, Jacob W; Muzykantov, Vladimir R; Reyes-Esteves, Sahily; Brenner, Jacob S

Olverembatinib After Failure of Tyrosine Kinase Inhibitors, Including Ponatinib or Asciminib: A Phase 1b Randomized Clinical Trial

奥维瑞巴替尼用于酪氨酸激酶抑制剂(包括帕纳替尼或阿西米尼)治疗失败后的疗效:一项 1b 期随机临床试验

Jabbour, Elias; Oehler, Vivian G; Koller, Paul B; Jamy, Omer; Lomaia, Elza; Hunter, Anthony M; Uspenskaya, Olga; Samarina, Svetlana; Mukherjee, Sudipto; Cortes, Jorge E; Baer, Maria R; Zherebtsova, Vera; Shuvaev, Vasily; Turkina, Anna; Davydkin, Igor; Guo, Huanshan; Chen, Zi; Fu, Tommy; Jiang, Lixin; Wang, Cunlin; Wang, Hengbang; Yang, Dajun; Zhai, Yifan; Kantarjian, Hagop

CD47 peptide-cloaked lipid nanoparticles promote cell-specific mRNA delivery

CD47肽包裹的脂质纳米颗粒促进细胞特异性mRNA递送

Papp, Tyler Ellis; Zeng, Jianhao; Shahnawaz, Hamna; Akyianu, Awurama; Breda, Laura; Yadegari, Amir; Steward, Joseph; Shi, Ruiqi; Li, Qin; Mui, Barbara L; Tam, Ying K; Weissman, Drew; Rivella, Stefano; Shuvaev, Vladimir; Muzykantov, Vladimir R; Parhiz, Hamideh

Systemic delivery of biotherapeutic RNA to the myocardium transiently modulates cardiac contractility in vivo.

将生物治疗性 RNA 系统性输送至心肌可暂时性地调节体内心脏收缩力

Shuvaev Vladimir V, Tam Ying K, Lee Benjamin W, Myerson Jacob W, Herbst Alan, Kiseleva Raisa Yu, Glassman Patrick M, Parhiz Hamideh, Alameh Mohamad-Gabriel, Pardi Norbert, Muramatsu Hiromi, Shuvaeva Tea I, Arguiri Evguenia, Marcos-Contreras Oscar A, Hood Elizabeth D, Brysgel Taylor V, Nong Jia, Papp Tyler E, Eaton Deborah M, Riley Rachel, Palanki Rohan, Musunuru Kiran, Brenner Jacob S, Mitchell Michael J, Ferrari Victor A, Mui Barbara L, Semple Sean C, Weppler Sherry A, Atluri Pavan, Margulies Kenneth B, Weissman Drew, Muzykantov Vladimir R

Phase-1 study of vamotinib (PF-114), a 3rd generation BCR::ABL1 tyrosine kinase-inhibitor, in chronic myeloid leukaemia

一项针对慢性粒细胞白血病患者的I期研究,评估了第三代BCR::ABL1酪氨酸激酶抑制剂vamotinib (PF-114)的疗效。

Turkina, Anna; Vinogradova, Olga; Lomaia, Elza; Shatokhina, Evgeniya; Shukhov, Oleg; Chelysheva, Ekaterina; Shikhbabaeva, Dzhariyat; Nemchenko, Irina; Petrova, Anna; Bykova, Anastasiya; Siordiya, Nadiya; Shuvaev, Vasily; Mikhailov, Ilya; Novikov, Fedor; Shulgina, Veronika; Hochhaus, Andreas; Ottmann, Oliver; Cortes, Jorge; Gale, Robert Peter; Chilov, Ghermes

Development of a fibrin-targeted theranostic for gastric cancer.

开发一种针对胃癌的纤维蛋白靶向诊疗一体化技术

Esfahani Shadi A, Ma Li, Krishna Shriya, Ma Hua, Raheem Shvan J, Shuvaev Sergey, Rotile Nicholas J, Weigand-Whittier Jonah, Boice Avery T, Borges Nicholas, Treaba Constantina A, Deffler Caitlin, Diyabalanage Himashinie, Humblet Valerie, Sosnovik David E, Mahmood Umar, Heidari Pedram, Shih Angela, Catana Ciprian, Strickland Matthew R, Klempner Samuel J, Caravan Peter

Collagen type I PET/MRI enables evaluation of treatment response in pancreatic cancer in pre-clinical and first-in-human translational studies

型胶原 PET/MRI 可在临床前和首次人体转化研究中评估胰腺癌的治疗反应

Shadi A Esfahani, Hua Ma, Shriya Krishna, Sergey Shuvaev, Mark Sabbagh, Caitlin Deffler, Nicholas Rotile, Jonah Weigand-Whittier, Iris Y Zhou, Ciprian Catana, Onofrio A Catalano, David T Ting, Pedram Heidari, Eric Abston, Michael Lanuti, Genevieve M Boland, Priyanka Pathak, Hannah Roberts, Kenneth K

Targeting lipid nanoparticles to the blood-brain barrier to ameliorate acute ischemic stroke

将脂质纳米颗粒靶向血脑屏障以改善急性缺血性卒中

Nong, Jia; Glassman, Patrick M; Shuvaev, Vladimir V; Reyes-Esteves, Sahily; Descamps, Helene C; Kiseleva, Raisa Y; Papp, Tyler E; Alameh, Mohamad-Gabriel; Tam, Ying K; Mui, Barbara L; Omo-Lamai, Serena; Zamora, Marco E; Shuvaeva, Tea; Arguiri, Evguenia; Gong, Xijing; Brysgel, Taylor V; Tan, Ai Wen; Woolfork, Ashley G; Weljie, Aalim; Thaiss, Christoph A; Myerson, Jacob W; Weissman, Drew; Kasner, Scott E; Parhiz, Hamideh; Muzykantov, Vladimir R; Brenner, Jacob S; Marcos-Contreras, Oscar A

Encoding innate ability through a genomic bottleneck

通过基因组瓶颈编码先天能力

Shuvaev, Sergey; Lachi, Divyansha; Koulakov, Alexei; Zador, Anthony

Physiologically based modeling of LNP-mediated delivery of mRNA in the vascular system

基于生理的 LNP 介导的血管系统中 mRNA 递送模型

Hamideh Parhiz, Vladimir V Shuvaev, Qin Li, Tyler E Papp, Awurama A Akyianu, Ruiqi Shi, Amir Yadegari, Hamna Shahnawaz, Sean C Semple, Barbara L Mui, Drew Weissman, Vladimir R Muzykantov, Patrick M Glassman