日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Age-sensitive response of systemic AAV-mediated gene therapy in a newly characterized feline model of mucolipidosis II.

在新鉴定的猫粘脂病 II 型模型中,系统性 AAV 介导的基因治疗的年龄敏感性反应

Pyne Nettie K, Bagel Jessica, Shyng Charles, Odonnell Patricia, Miyadera Keiko, Srnak Jennifer, Swain Gary, Pesayco Jill P, Shelton G Diane, Assenmacher Charles-Antoine, Dickson Patricia, Stern Joshua A, Flanagan-Steet Heather, Gray Steven J, Bradbury Allison M

Dual-isoform hUBE3A gene transfer improves behavioral and seizure outcomes in Angelman syndrome model mice

双亚型 hUBE3A 基因转移改善了 Angelman 综合征模型小鼠的行为和癫痫发作情况

Judson, Matthew C; Shyng, Charles; Simon, Jeremy M; Davis, Courtney R; Punt, A Mattijs; Salmon, Mirabel T; Miller, Noah W; Ritola, Kimberly D; Elgersma, Ype; Amaral, David G; Gray, Steven J; Philpot, Benjamin D

Recent progress and considerations for AAV gene therapies targeting the central nervous system

针对中枢神经系统的AAV基因疗法的最新进展和考量

Lykken, Erik Allen; Shyng, Charles; Edwards, Reginald James; Rozenberg, Alejandra; Gray, Steven James

Histochemical localization of palmitoyl protein thioesterase-1 activity

棕榈酰蛋白硫酯酶-1活性的组织化学定位

Dearborn, Joshua T; Ramachandran, Subramania; Shyng, Charles; Lu, Jui-Yun; Thornton, Jonah; Hofmann, Sandra L; Sands, Mark S

An anti-neuroinflammatory that targets dysregulated glia enhances the efficacy of CNS-directed gene therapy in murine infantile neuronal ceroid lipofuscinosis

一种靶向失调神经胶质细胞的抗神经炎症药物可增强中枢神经系统靶向基因疗法在小鼠婴儿神经元蜡样脂褐质沉积症中的疗效。

Macauley, Shannon L; Wong, Andrew M S; Shyng, Charles; Augner, David P; Dearborn, Joshua T; Pearse, Yewande; Roberts, Marie S; Fowler, Stephen C; Cooper, Jonathan D; Watterson, D Martin; Sands, Mark S