日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Systematic Review: Efficacy of Medical Therapy on Outcomes Important to Adult Patients With X-Linked Hypophosphatemia

系统评价:药物治疗对X连锁低磷血症成年患者重要结局的疗效

Ali, Dalal S; Mirza, Reza D; Alsarraf, Farah; Hussein, Salma; Abu Alrob, Hajar; Appelman-Dijkstra, Natasha M; Beck-Nielsen, Signe Sparre; Biosse-Duplan, Martin; Brandi, Maria Luisa; Carpenter, Thomas O; Chaussain, Catherine; Cohen-Solal, Martine; Crowley, Rachel K; Dandurand, Karel; Florenzano, Pablo; Fukumoto, Seiji; Gagnon, Claudia; Goodyer, Paul; Grasemann, Corinna; Imel, Erik A; Jan de Beur, Suzanne M; Lehman, Anna; Lewiecki, E Michael; Morgante, Emmett; Ward, Leanne M; Khan, Aliya A; Guyatt, Gordon

X-Linked Hypophosphatemia Management in Children: An International Working Group Clinical Practice Guideline

儿童X连锁低磷血症的管理:国际工作组临床实践指南

Ali, Dalal S; Carpenter, Thomas O; Imel, Erik A; Ward, Leanne M; Appelman-Dijkstra, Natasha M; Chaussain, Catherine; Jan de Beur, Suzanne M; Florenzano, Pablo; Abu Alrob, Hajar; Aldabagh, Rana; Alexander, R Todd; Alsarraf, Farah; Beck-Nielsen, Signe Sparre; Biosse-Duplan, Martin; Crowley, Rachel K; Dandurand, Karel; Filler, Guido; Friedlander, Lisa; Fukumoto, Seiji; Gagnon, Claudia; Goodyer, Paul; Grasemann, Corinna; Grimbly, Chelsey; Hussein, Salma; Javaid, Muhammad K; Khan, Sarah; Khan, Aneal; Lehman, Anna; Lems, Willem F; Lewiecki, E Michael; McDonnell, Ciara; Mirza, Reza D; Morgante, Emmett; Morrison, Archibald; Portale, Anthony A; Rao, Christina; Rhee, Yumie; Rush, Eric T; Siggelkow, Heide; Tetradis, Sotirios; Tosi, Laura; Guyatt, Gordon; Brandi, Maria Luisa; Khan, Aliya A

Current Practices in Monitoring Children and Adults With X-linked Hypophosphatemia: A Global Survey of Expert Experience

目前对患有X连锁低磷血症的儿童和成人进行监测的实践:一项全球专家经验调查

Ali, Dalal S; Alsarraf, Farah; Alrob, Hajar Abu; Alexander, R Todd; Almoulia, Abdulrahman; Appelman-Dijkstra, Natasha M; Beck-Nielsen, Signe Sparre; Biosse-Duplan, Martin; Brandi, Maria Luisa; Carpenter, Thomas O; Chaussain, Catherine; Cohen-Solal, Martine; Crowley, Rachel K; Dandurand, Karel; Florenzano, Pablo; Gagnon, Claudia; Goodyer, Paul; Grimbly, Chelsey; Hussein, Salma; Imel, Erik A; Jan de Beur, Suzanne M; Javaid, Muhammad K; Lehman, Anna; Lems, Willem F; Lewiecki, E Michael; McDonnell, Ciara; Mirza, Reza D; Morgante, Emmett; Portale, Anthony A; Rhee, Yumie; Siggelkow, Heide; Tosi, Laura L; Ward, Leanne M; Guyatt, Gordon; Khan, Aliya A

X-Linked Hypophosphatemia Management in Adults: An International Working Group Clinical Practice Guideline

成人X连锁低磷血症的管理:国际工作组临床实践指南

Khan, Aliya A; Ali, Dalal S; Appelman-Dijkstra, Natasha M; Carpenter, Thomas O; Chaussain, Catherine; Imel, Erik A; Jan de Beur, Suzanne M; Florenzano, Pablo; Abu Alrob, Hajar; Aldabagh, Rana; Alexander, R Todd; Alsarraf, Farah; Beck-Nielsen, Signe Sparre; Biosse-Duplan, Martin; Cohen-Solal, Martine; Crowley, Rachel K; Dandurand, Karel; Filler, Guido; Friedlander, Lisa; Fukumoto, Seiji; Gagnon, Claudia; Goodyer, Paul; Grasemann, Corinna; Grimbly, Chelsey; Hussein, Salma; Javaid, Muhammad K; Khan, Sarah; Khan, Aneal; Lehman, Anna; Lems, Willem F; Lewiecki, E Michael; McDonnell, Ciara; Mirza, Reza D; Morgante, Emmett; Morrison, Archibald; Portale, Anthony A; Rhee, Yumie; Rush, Eric T; Siggelkow, Heide; Tetradis, Sotirios; Tosi, Laura; Ward, Leanne M; Guyatt, Gordon; Brandi, Maria Luisa

XLH Matters: an evolving programme to discuss new advances and share clinical experiences to improve patient outcomes

XLH Matters:一个不断发展的项目,旨在探讨最新进展并分享临床经验,以改善患者预后。

Seefried, Lothar; Aliberti, Ferdinando; Heier, Cathrine Alsaker; Arango-Sancho, Pedro; Biosse Duplan, Martin; Sakka, Sophia D; Emma, Francesco; Gardiner, Oliver; Javaid, Muhammad Kassim; Ferreira-Santos, Rui M; Raimann, Adalbert; Rak, Kristen; Bubbear, Judith S; Cheung, Moira S; Beck-Nielsen, Signe Sparre; Mindler, Gabriel T; Linglart, Agnès

XLH Matters 2024: expert insights and practical tools for enhancing care of people living with X-linked hypophosphataemia

XLH Matters 2024:专家见解和实用工具,旨在改善X连锁低磷血症患者的护理

Seefried, Lothar; Alzahrani, Ali S; Wagner, Carsten A; Eade, Damian; Fintini, Danilo; Haffner, Dieter; Frookh Jamal, Hasan; Bubbear, Judith S; Guazzarotti, Laura; Cheung, Moira S; Abid, Noina; Costa-Reis, Patrícia; Ferreira Santos, Rui; Beck-Nielsen, Signe Sparre; Linglart, Agnès

Higher bone mineral density at six years of age in very preterm-born infants fed human milk compared to formula feeding. A secondary analysis of an RCT

与配方奶喂养相比,母乳喂养的极早产儿在六岁时骨密度更高。这是对一项随机对照试验的二次分析。

Toftlund, Line H; Beck-Nielsen, Signe Sparre; Agertoft, Lone; Halken, Susanne; Zachariassen, Gitte

Correction to: Higher bone mineral density at six years of age in very preterm-born infants fed human milk compared to formula feeding. A secondary analysis of an RCT

更正:与配方奶喂养相比,母乳喂养的极早产儿在六岁时骨密度更高。一项随机对照试验的二次分析

Toftlund, Line H; Beck-Nielsen, Signe Sparre; Agertoft, Lone; Halken, Susanne; Zachariassen, Gitte

Increased lifelong burden of comorbidities without increased early mortality in hereditary hypophosphatemia: a Danish register study

遗传性低磷血症患者终生合并症负担增加,但早期死亡率并未增加:一项丹麦登记研究

Beck-Nielsen, Signe Sparre; Hansen, Rikke Færgemann; Johansen, Ulla Ege; Williams, Angela

Real-world non-interventional post-authorization safety study of long-term use of burosumab in children and adolescents with X-linked hypophosphatemia: first interim analysis

一项真实世界、非干预性上市后安全性研究,评估布罗索单抗长期用于治疗X连锁低磷血症儿童和青少年的安全性:首次中期分析

Boot, Annemieke M; Ariceta, Gema; Beck-Nielsen, Signe Sparre; Brandi, Maria Luisa; Briot, Karine; Collantes, Carmen de Lucas; Giannini, Sandro; Haffner, Dieter; Keen, Richard; Levtchenko, Elena; Mughal, M Zulf; Mӓkitie, Outi; Nilsson, Ola; Schnabel, Dirk; Tripto-Shkolnik, Liana; Zillikens, M Carola; Liu, Jonathan; Tudor, Alina; Emma, Francesco