A framework for individualized splice-switching oligonucleotide therapy
个体化剪接转换寡核苷酸治疗框架
期刊:Nature
影响因子:50.5
doi:10.1038/s41586-023-06277-0
Jinkuk Kim #, Sijae Woo #, Claudio M de Gusmao #, Boxun Zhao #, Diana H Chin, Renata L DiDonato, Minh A Nguyen, Tojo Nakayama, Chunguang April Hu, Aubrie Soucy, Ashley Kuniholm, Jennifer Karlin Thornton, Olivia Riccardi, Danielle A Friedman, Christelle Moufawad El Achkar, Zane Dash, Laura Cornelisse