Partial correction of immunodeficiency by lentiviral vector gene therapy in mouse models carrying Rag1 hypomorphic mutations
慢病毒载体基因治疗对携带Rag1亚效等位基因突变的小鼠模型部分纠正免疫缺陷
期刊:Frontiers in Immunology
影响因子:5.7
doi:10.3389/fimmu.2023.1268620
Maria Carmina Castiello #, Martina Di Verniere #, Elena Draghici, Elena Fontana, Sara Penna, Lucia Sereni, Alessandra Zecchillo, Denise Minuta, Paolo Uva, Marco Zahn, Irene Gil-Farina, Andrea Annoni, Silvia Iaia, Lisa M Ott de Bruin, Luigi D Notarangelo, Karin Pike-Overzet, Frank J T Staal, Anna Vil