Impaired prenatal motor axon development necessitates early therapeutic intervention in severe SMA
严重脊髓性肌萎缩症(SMA)中,产前运动轴突发育受损需要早期治疗干预。
期刊:Science Translational Medicine
影响因子:14.6
doi:10.1126/scitranslmed.abb6871
Kong, Lingling; Valdivia, David O; Simon, Christian M; Hassinan, Cera W; Delestrée, Nicolas; Ramos, Daniel M; Park, Jae Hong; Pilato, Celeste M; Xu, Xixi; Crowder, Melissa; Grzyb, Chloe C; King, Zachary A; Petrillo, Marco; Swoboda, Kathryn J; Davis, Crystal; Lutz, Cathleen M; Stephan, Alexander H; Zhao, Xin; Weetall, Marla; Naryshkin, Nikolai A; Crawford, Thomas O; Mentis, George Z; Sumner, Charlotte J