Gene transfer of master autophagy regulator TFEB results in clearance of toxic protein and correction of hepatic disease in alpha-1-anti-trypsin deficiency
主自噬调节因子 TFEB 的基因转移可清除毒性蛋白质并纠正 α-1-抗胰蛋白酶缺乏症中的肝病
期刊:EMBO Molecular Medicine
影响因子:9
doi:10.1002/emmm.201202046
Nunzia Pastore, Keith Blomenkamp, Fabio Annunziata, Pasquale Piccolo, Pratibha Mithbaokar, Rosa Maria Sepe, Francesco Vetrini, Donna Palmer, Philip Ng, Elena Polishchuk, Simona Iacobacci, Roman Polishchuk, Jeffrey Teckman, Andrea Ballabio, Nicola Brunetti-Pierri