Newborn Screening for Spinal Muscular Atrophy in New York State: Clinical Outcomes From the First 3 Years
纽约州新生儿脊髓性肌萎缩症筛查:前三年的临床结果
期刊:Neurology
影响因子:8.5
doi:10.1212/WNL.0000000000200986
Lee, Bo Hoon; Deng, Stella; Chiriboga, Claudia A; Kay, Denise M; Irumudomon, Obehioya; Laureta, Emma; Delfiner, Leslie; Treidler, Simona O; Anziska, Yaacov; Sakonju, Ai; Kois, Chelsea; Farooq, Osman; Engelstad, Kristin; Laurenzano, Alexandra; Hogan, Katherine; Caggana, Michele; Saavedra-Matiz, Carlos A; Stevens, Colleen F; Ciafaloni, Emma