dCas9-Based Scn1a Gene Activation Restores Inhibitory Interneuron Excitability and Attenuates Seizures in Dravet Syndrome Mice
基于 dCas9 的 Scn1a 基因激活可恢复抑制性中间神经元兴奋性并减弱 Dravet 综合征小鼠的癫痫发作
期刊:Molecular Therapy
影响因子:12.1
doi:10.1016/j.ymthe.2019.08.018
Gaia Colasante, Gabriele Lignani, Simone Brusco, Claudia Di Berardino, Jenna Carpenter, Serena Giannelli, Nicholas Valassina, Simone Bido, Raffaele Ricci, Valerio Castoldi, Silvia Marenna, Timothy Church, Luca Massimino, Giuseppe Morabito, Fabio Benfenati, Stephanie Schorge, Letizia Leocani, Dimitri