Targeted CNS Delivery Using Human MiniPromoters and Demonstrated Compatibility with Adeno-Associated Viral Vectors
使用人类 MiniPromoters 进行中枢神经系统靶向递送并证明与腺相关病毒载体的兼容性
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:
doi:10.1038/mtm.2013.5
Charles N de Leeuw, Frank M Dyka, Sanford L Boye, Stéphanie Laprise, Michelle Zhou, Alice Y Chou, Lisa Borretta, Simone C McInerny, Kathleen G Banks, Elodie Portales-Casamar, Magdalena I Swanson, Cletus A D'Souza, Shannon E Boye, Steven J M Jones, Robert A Holt, Daniel Goldowitz, William W Hauswirth