Baboon Envelope Pseudotyped "Nanoblades" Carrying Cas9/gRNA Complexes Allow Efficient Genome Editing in Human T, B, and CD34+ Cells and Knock-in of AAV6-Encoded Donor DNA in CD34+ Cells
携带 Cas9/gRNA 复合物的狒狒包膜假型“纳米刀片”可在人类 T、B 和 CD34+ 细胞中进行有效的基因组编辑,并在 CD34+ 细胞中敲入 AAV6 编码的供体 DNA
期刊:Frontiers in Genome Editing
影响因子:4.9
doi:10.3389/fgeed.2021.604371
Alejandra Gutierrez-Guerrero, Maria Jimena Abrey Recalde, Philippe E Mangeot, Caroline Costa, Ornellie Bernadin, Séverine Périan, Floriane Fusil, Gisèle Froment, Adriana Martinez-Turtos, Adrien Krug, Francisco Martin, Karim Benabdellah, Emiliano P Ricci, Simone Giovannozzi, Rik Gijsbers, Eduard Ayus