Safe and effective liver-directed AAV-mediated homology-independent targeted integration in mouse models of inherited diseases
在遗传疾病小鼠模型中安全有效的肝脏定向 AAV 介导的同源性非依赖性靶向整合
期刊:Cell Reports Medicine
影响因子:11.7
doi:10.1016/j.xcrm.2024.101619
Federica Esposito, Fabio Dell'Aquila, Manuel Rhiel, Stefano Auricchio, Kay Ole Chmielewski, Geoffroy Andrieux, Rita Ferla, Paula Sureda Horrach, Arjun Padmanabhan, Roberto Di Cunto, Simone Notaro, Manel Llado Santeularia, Melanie Boerries, Margherita Dell'Anno, Edoardo Nusco, Agnese Padula, Sofia Nu
