日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Streamlined, single-step non-viral CRISPR-Cas9 knockout strategy enhances gene editing efficiency in primary human chondrocyte populations

简化的单步非病毒 CRISPR-Cas9 基因敲除策略提高了原代人软骨细胞群的基因编辑效率

Simone Ponta # ,Angela Bonato # ,Philipp Neidenbach ,Valentino F Bruhin ,Alexis Laurent ,Lee Ann Applegate ,Marcy Zenobi-Wong ,Goncalo Barreto

Engineering Inflammation-Resistant Cartilage: Bridging Gene Therapy and Tissue Engineering

工程抗炎软骨:桥接基因治疗和组织工程

Angela Bonato, Philipp Fisch, Simone Ponta, David Fercher, Mikko Manninen, Daniel Weber, Kari K Eklund, Goncalo Barreto, Marcy Zenobi-Wong

Engineering of the endogenous HBD promoter increases HbA2

内源性 HBD 启动子工程可增加 HbA2

Mandy Y Boontanrart, Elia Mächler, Simone Ponta, Jan C Nelis, Viviana G Preiano, Jacob E Corn