Improvement of bone disease by imiglucerase (Cerezyme) therapy in patients with skeletal manifestations of type 1 Gaucher disease: results of a 48-month longitudinal cohort study
伊米苷酶(Cerezyme)治疗改善1型戈谢病骨骼表现患者的骨骼疾病:一项为期48个月的纵向队列研究结果
期刊:Clinical Genetics
影响因子:2.3
doi:10.1111/j.1399-0004.2008.00978.x
Sims, K B; Pastores, G M; Weinreb, N J; Barranger, J; Rosenbloom, B E; Packman, S; Kaplan, P; Mankin, H; Xavier, R; Angell, J; Fitzpatrick, M A; Rosenthal, D