AAV-Mediated Progranulin Delivery to a Mouse Model of Progranulin Deficiency Causes T Cell-Mediated Toxicity
AAV 介导的颗粒蛋白前体向颗粒蛋白前体缺乏的小鼠模型递送会导致 T 细胞介导的毒性
期刊:Molecular Therapy
影响因子:12.1
doi:10.1016/j.ymthe.2018.11.013
Defne A Amado, Julianne M Rieders, Fortunay Diatta, Pilar Hernandez-Con, Adina Singer, Jordan T Mak, Junxian Zhang, Eric Lancaster, Beverly L Davidson, Alice S Chen-Plotkin