日期 影响因子
日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:
–

Efficacy of Acoramidis in Wild-Type and Variant Transthyretin Amyloid Cardiomyopathy: Results From ATTRibute-CM and Its Open-Label Extension

Acoramidis治疗野生型和变异型转甲状腺素蛋白淀粉样变性心肌病的疗效：来自ATTRibute-CM及其开放标签扩展研究的结果

期刊:Jama Cardiology
影响因子:14.1
doi:10.1001/jamacardio.2025.4477
Alexander, Kevin M; Davis, Margot K; Akinboboye, Olakunle; Berk, John; Bhatt, Kunal; Cappelli, Francesco; Cuddy, Sarah A M; Fontana, Marianna; Garcia-Pavia, Pablo; Gillmore, Julian D; Griffin, Jan M; Grodin, Justin L; Judge, Daniel P; Khouri, Michel G; Lam, Kaitlyn; Masri, Ahmad; Maurer, Mathew S; Obici, Laura; Ruberg, Frederick L; Sarswat, Nitasha; Shah, Keyur; Soman, Prem; Stern, Lily; Wright, Richard; Xiong, Kuangnan; Cao, Xiaofan; Lystig, Ted; Tamby, Jean-François; Castaño, Adam; Katz, Leonid; Sinha, Uma; Fox, Jonathan C; Solomon, Scott D; Grogan, Martha
心血管
心肌病
免疫/内分泌
发表日期：2026
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Long-Term Durability of Acoramidis Efficacy in Transthyretin Amyloid Cardiomyopathy: Open-Label Extension of the ATTRibute-CM Randomized Clinical Trial

Acoramidis治疗转甲状腺素蛋白淀粉样变性心肌病的长期疗效：ATTRibute-CM随机临床试验的开放标签扩展研究

期刊:Jama Cardiology
影响因子:14.1
doi:10.1001/jamacardio.2026.0819
Soman, Prem; Cuddy, Sarah A M; Gillmore, Julian D; Sarswat, Nitasha; Judge, Daniel P; Cappelli, Francesco; Stern, Lily K; Wright, Richard; Akinboboye, Olakunle; Obici, Laura; Bhatt, Kunal; Xiong, Kuangnan; Castaño, Adam; Chen, Chris; Falvey, Heather; Pecoraro, Maria Lucia; Tamby, Jean-François; Sinha, Uma; Fox, Jonathan C; Shah, Keyur; Grodin, Justin L; Ambardekar, Amrut V; Alexander, Kevin M; Khouri, Michel G; Cheng, Richard K
心血管
心肌病
免疫/内分泌
发表日期：2026
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Long-Term Efficacy and Safety of Acoramidis in ATTR-CM: Initial Report From the Open-Label Extension of the ATTRibute-CM Trial

Acoramidis治疗ATTR-CM的长期疗效和安全性：ATTRibute-CM试验开放标签扩展研究的初步报告

期刊:Circulation
影响因子:38.6
doi:10.1161/CIRCULATIONAHA.124.072771
Judge, Daniel P; Gillmore, Julian D; Alexander, Kevin M; Ambardekar, Amrut V; Cappelli, Francesco; Fontana, Marianna; García-Pavía, Pablo; Grodin, Justin L; Grogan, Martha; Hanna, Mazen; Masri, Ahmad; Nativi-Nicolau, Jose; Obici, Laura; Hvitfeldt Poulsen, Steen; Sarswat, Nitasha; Shah, Keyur; Soman, Prem; Lystig, Ted; Cao, Xiaofan; Wang, Kevin; Pecoraro, Maria Lucia; Tamby, Jean-François; Katz, Leonid; Sinha, Uma; Fox, Jonathan C; Maurer, Mathew S
发表日期：2025
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Differential Binding Affinities and Kinetics of Transthyretin Stabilizers

转甲状腺素蛋白稳定剂的差异性结合亲和力和动力学

期刊:Journal of Cardiovascular Pharmacology
影响因子:2.2
doi:10.1097/FJC.0000000000001726
Ji, Alan X; Betz, Andreas; Sinha, Uma
免疫/内分泌
发表日期：2025
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A plain language review of the ATTRibute-CM study: efficacy and safety of acoramidis in transthyretin amyloid cardiomyopathy

ATTRibute-CM 研究的简明语言综述：acoramidis 治疗转甲状腺素蛋白淀粉样变性心肌病的疗效和安全性

期刊:Future Cardiology
影响因子:1
doi:10.1080/14796678.2025.2591426
Gillmore, Julian D; Judge, Daniel P; Cappelli, Francesco; Fontana, Marianna; Garcia-Pavia, Pablo; Gibbs, Simon; Grogan, Martha; Hanna, Mazen; Hoffman, James; Masri, Ahmad; Maurer, Mathew S; Nativi-Nicolau, Jose; Obici, Laura; Poulsen, Steen Hvitfeldt; Rockhold, Frank; Shah, Keyur B; Soman, Prem; Garg, Jyotsna; Chiswell, Karen; Xu, Haolin; Cao, Xiaofan; Lystig, Ted; Sinha, Uma; Fox, Jonathan C
心血管
心肌病
免疫/内分泌
发表日期：2025
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Correction to: Validation of a novel western blot assay to monitor patterns and levels of alpha dystroglycan in skeletal muscle of patients with limb girdle muscular dystrophies

更正：验证一种新型蛋白质印迹法检测肢带型肌营养不良症患者骨骼肌中α-肌营养不良蛋白聚糖的模式和水平

期刊:Journal of Muscle Research and Cell Motility
影响因子:1.7
doi:10.1007/s10974-024-09678-4
Rajasingham, Thulashitha; Rodriguez, Hector M; Betz, Andreas; Sproule, Douglas M; Sinha, Uma
WB
发表日期：2024
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First-in-Human Study of AG10, a Novel, Oral, Specific, Selective, and Potent Transthyretin Stabilizer for the Treatment of Transthyretin Amyloidosis: A Phase 1 Safety, Tolerability, Pharmacokinetic, and Pharmacodynamic Study in Healthy Adult Volunteers

AG10（一种新型口服、特异性、选择性强效的转甲状腺素蛋白稳定剂）治疗转甲状腺素蛋白淀粉样变性的首次人体研究：一项在健康成年志愿者中进行的 1 期安全性、耐受性、药代动力学和药效学研究

期刊:Clinical Pharmacology in Drug Development
影响因子:1.8
doi:10.1002/cpdd.700
Fox, Jonathan C; Hellawell, Jennifer L; Rao, Satish; O'Reilly, Terry; Lumpkin, Rick; Jernelius, Jesper; Gretler, Daniel; Sinha, Uma
Human
免疫/内分泌
发表日期：2020
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Heparin rescues factor V Leiden-associated placental failure independent of anticoagulation in a murine high-risk pregnancy model

在小鼠高危妊娠模型中，肝素可独立于抗凝治疗挽救V因子Leiden相关的胎盘功能衰竭。

期刊:Blood
影响因子:23.1
doi:10.1182/blood-2012-08-448209
An, Jianzhong; Waitara, Magarya S; Bordas, Michelle; Arumugam, Vidhyalakshmi; Hoffmann, Raymond G; Petrich, Brian G; Sinha, Uma; North, Paula E; Sood, Rashmi
发表日期：2013
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Methotrexate and a spleen tyrosine kinase inhibitor cooperate to inhibit responses to peripheral blood B cells in rheumatoid arthritis.

甲氨蝶呤和脾酪氨酸激酶抑制剂协同作用，抑制类风湿性关节炎患者外周血 B 细胞的反应

期刊:Pharmacology Research & Perspectives
影响因子:2.3
doi:10.1002/prp2.16
Coffey Greg, Betz Andreas, Graf Jonathan, Stephens Gillian, Hua Lin Pei, Imboden John, Sinha Uma
细胞生物学
关节炎
炎症
发表日期：2013
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Acromegaly without acral changes: A rare presentation

无肢端改变的肢端肥大症：一种罕见的表现

期刊:Indian Journal of Endocrinology and Metabolism
影响因子:
doi:10.4103/2230-8210.95713
Sengupta, Nilanjan; Sinha, Uma; Roy, Keshab Sinha; Saha, Sudipta
发表日期：2012
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