Reengineering a receptor footprint of adeno-associated virus enables selective and systemic gene transfer to muscle
通过对腺相关病毒受体足迹进行重新设计,可以实现对肌肉的选择性和系统性基因转移。
期刊:Nature Biotechnology
影响因子:41.7
doi:10.1038/nbt.1599
Asokan, Aravind; Conway, Julia C; Phillips, Jana L; Li, Chengwen; Hegge, Julia; Sinnott, Rebecca; Yadav, Swati; DiPrimio, Nina; Nam, Hyun-Joo; Agbandje-McKenna, Mavis; McPhee, Scott; Wolff, Jon; Samulski, R Jude