Correction: Long-term safety and efficacy of cipaglucosidase alfa plus miglustat in individuals living with Pompe disease: an open-label phase I/II study (ATB200-02)
更正:西帕葡萄糖苷酶α联合米格司他治疗庞贝病患者的长期安全性和有效性:一项开放标签I/II期研究(ATB200-02)
期刊:Journal of Neurology
影响因子:4.6
doi:10.1007/s00415-025-12899-3
Byrne, Barry J; Schoser, Benedikt; Kishnani, Priya S; Bratkovic, Drago; Clemens, Paula R; Goker-Alpan, Ozlem; Ming, Xue; Roberts, Mark; Vorgerd, Matthias; Sivakumar, Kumaraswamy; van der Ploeg, Ans T; Goldman, Mitchell; Wright, Jacquelyn; Holdbrook, Fred; Jain, Vipul; Benjamin, Elfrida R; Johnson, Franklin; Das, Sheela Sitaraman; Wasfi, Yasmine; Mozaffar, Tahseen