The ARCA Registry: A Collaborative Global Platform for Advancing Trial Readiness in Autosomal Recessive Cerebellar Ataxias
ARCA注册库:推进常染色体隐性小脑共济失调临床试验准备工作的全球合作平台
期刊:Frontiers in Neurology
影响因子:2.8
doi:10.3389/fneur.2021.677551
Traschütz, Andreas; Reich, Selina; Adarmes, Astrid D; Anheim, Mathieu; Ashrafi, Mahmoud Reza; Baets, Jonathan; Basak, A Nazli; Bertini, Enrico; Brais, Bernard; Gagnon, Cynthia; Gburek-Augustat, Janina; Hanagasi, Hasmet A; Heinzmann, Anna; Horvath, Rita; de Jonghe, Peter; Kamm, Christoph; Klivenyi, Peter; Klopstock, Thomas; Minnerop, Martina; Münchau, Alexander; Renaud, Mathilde; Roxburgh, Richard H; Santorelli, Filippo M; Schirinzi, Tommaso; Sival, Deborah A; Timmann, Dagmar; Vielhaber, Stefan; Wallner, Michael; van de Warrenburg, Bart P; Zanni, Ginevra; Zuchner, Stephan; Klockgether, Thomas; Schüle, Rebecca; Schöls, Ludger; Synofzik, Matthis