CRISPR/Cas9 mediated generation of an ovine model for infantile neuronal ceroid lipofuscinosis (CLN1 disease)
利用 CRISPR/Cas9 技术构建绵羊婴儿神经元蜡样脂褐质沉积症(CLN1 病)模型
期刊:Scientific Reports
影响因子:3.9
doi:10.1038/s41598-019-45859-9
Eaton, S L; Proudfoot, C; Lillico, S G; Skehel, P; Kline, R A; Hamer, K; Rzechorzek, N M; Clutton, E; Gregson, R; King, T; O'Neill, C A; Cooper, J D; Thompson, G; Whitelaw, C B; Wishart, T M