Elevated tripeptidyl-peptidase 1 corrects multiple disease phenotypes in a mouse model of juvenile neuronal ceroid lipofuscinosis
三肽基肽酶 1 水平升高可纠正幼年神经元蜡样脂褐质沉积症小鼠模型中的多种疾病表型
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2025.101587
Banach-Petrosky, Whitney; Larrimore, Katherine E; Sleat, Elizabeth H; Bazer, Allyson; Samuels, Benjamin; Tan, Yalun; Melton, Andrew C; Ichida, Justin K; Logan, Todd P; Lobel, Peter; Sleat, David E