日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

CISH, a key intracellular checkpoint, in comparison and combination to existing and emerging cancer immune checkpoints

CISH,一种关键的细胞内检查点,与现有和新兴的癌症免疫检查点进行比较和组合

Florencia Cano,Alberto Bravo-Blas,Mathilde Colombe,Chiara Cerrato,Ram Kumar Chowdary Venigalla,Olivier Preham,Ellie Burns,Paige Mortimer,Aalia Choudhry,Nicholas Slipek,Matthew J Johnson,Beau R Webber,Branden S Moriarity,Emil Lou,Modassir Choudhry,Christopher A Klebanoff,Tom Henley

Precision enhancement of CAR-NK cells through non-viral engineering and highly multiplexed base editing.

通过非病毒工程和高通量碱基编辑实现CAR-NK细胞的精确增强

Wang Minjing, Krueger Joshua B, Gilkey Alexandria K, Stelljes Erin M, Kluesner Mitchell G, Pomeroy Emily J, Skeate Joseph G, Slipek Nicholas J, Lahr Walker S, Claudio Vázquez Patricia N, Zhao Yueting, Bell Jason B, Clement Kendell, Eaton Ella J, Laoharawee Kanut, Chang Jae-Woong, Webber Beau R, Moriarity Branden S

Installation of dominant-negative mutations in FAS and TGFβR2 via base editing in primary T cells

通过碱基编辑在原代T细胞中引入FAS和TGFβR2的显性负突变

Bryce J Wick ,Mitchell G Kluesner ,Nicholas J Slipek ,Joseph G Skeate ,Ethan M Niemeyer ,Beau R Webber ,Branden S Moriarity

Installation of Dominant-Negative Mutations in FAS and TGFβR2 via Base Editing in Primary T Cells.

通过碱基编辑在原代 T 细胞中引入 FAS 和 TGFβR2 的显性负突变。

Wick Bryce J, Kluesner Mitchell G, Slipek Nicholas J, Skeate Joseph G, Niemeyer Ethan M, Webber Beau R, Moriarity Branden S

A Singular Base Editing Platform for Polyfunctional Multiplex Engineering of Immune Cells.

用于免疫细胞多功能多重工程的单一碱基编辑平台

Skeate Joseph G, Slipek Nicholas J, Lahr Walker S, Roy Shambojit, Wick Bryce J, Stelljes Erin M, Gilkey Alexandria K, Thenge Prateek P, Diers Miechaleen D, Kar Bibekananda, Krueger Joshua B, Niemeyer Ethan M, Lonetree Cara-Lin, Kluesner Mitchell G, Bell Jason B, Clement Kendell, Provenzano Paolo, Moriarity Branden S, Webber Beau R

Cas9-induced targeted integration of large DNA payloads in primary human T cells via homology-mediated end-joining DNA repair

Cas9 通过同源介导的末端连接 DNA 修复诱导人类原代 T 细胞中大型 DNA 有效载荷的靶向整合

Beau R Webber #, Matthew J Johnson #, Joseph G Skeate, Nicholas J Slipek, Walker S Lahr, Anthony P DeFeo, Lauren J Mills, Xiaohong Qiu, Blaine Rathmann, Miechaleen D Diers, Bryce Wick, Tom Henley, Modassir Choudhry, Timothy K Starr, R Scott McIvor, Branden S Moriarity2

Engineering memory T cells as a platform for long-term enzyme replacement therapy in lysosomal storage disorders

设计记忆 T 细胞作为溶酶体贮积症长期酶替代疗法的平台

Evan W Kleinboehl, Kanut Laoharawee, Jacob D Jensen, Joseph J Peterson, Nicholas J Slipek, Bryce J Wick, Matthew J Johnson, Beau R Webber, Branden S Moriarity

Evolution of the clinical-stage hyperactive TcBuster transposase as a platform for robust non-viral production of adoptive cellular therapies.

临床阶段高活性 TcBuster 转座酶的演变,使其成为强大的非病毒过继细胞疗法生产的平台

Skeate Joseph G, Pomeroy Emily J, Slipek Nicholas J, Jones Bryan J, Wick Bryce J, Chang Jae-Woong, Lahr Walker S, Stelljes Erin M, Patrinostro Xiaobai, Barnes Blake, Zarecki Trevor, Krueger Joshua B, Bridge Jacob E, Robbins Gabrielle M, McCormick Madeline D, Leerar John R, Wenzel Kari T, Hornberger Kathlyn M, Walker Kirsti, Smedley Dalton, Largaespada David A, Otto Neil, Webber Beau R, Moriarity Branden S

Engineering Memory T Cells as a platform for Long-Term Enzyme Replacement Therapy in Lysosomal Storage Disorders

利用工程化记忆T细胞作为溶酶体贮积症长期酶替代疗法的平台

Laoharawee, Kanut; Kleinboehl, Evan W; Jensen, Jacob D; Peterson, Joseph J; Slipek, Nicholas J; Wick, Bryce J; Johnson, Matthew J; Webber, Beau R; Moriarity, Branden S

Precision Enhancement of CAR-NK Cells through Non-Viral Engineering and Highly Multiplexed Base Editing

通过非病毒工程和高度多路复用的碱基编辑提高 CAR-NK 细胞的精准度

Minjing Wang, Joshua B Krueger, Alexandria K Gilkey, Erin M Stelljes, Mitchell G Kluesner, Emily J Pomeroy, Joseph G Skeate, Nicholas J Slipek, Walker S Lahr, Patricia N Claudio Vázquez, Yueting Zhao, Ella J Eaton, Kanut Laoharawee, Beau R Webber, Branden S Moriarity