Patient-Reported Outcomes from a Randomized, Active-Controlled, Open-Label, Phase 3 Trial of Burosumab Versus Conventional Therapy in Children with X-Linked Hypophosphatemia
一项随机、活性对照、开放标签的3期临床试验中,布罗索单抗与常规疗法治疗X连锁低磷血症患儿的患者报告结局
期刊:Calcified Tissue International
影响因子:3.2
doi:10.1007/s00223-020-00797-x
Padidela, Raja; Whyte, Michael P; Glorieux, Francis H; Munns, Craig F; Ward, Leanne M; Nilsson, Ola; Portale, Anthony A; Simmons, Jill H; Namba, Noriyuki; Cheong, Hae Il; Pitukcheewanont, Pisit; Sochett, Etienne; Högler, Wolfgang; Muroya, Koji; Tanaka, Hiroyuki; Gottesman, Gary S; Biggin, Andrew; Perwad, Farzana; Williams, Angela; Nixon, Annabel; Sun, Wei; Chen, Angel; Skrinar, Alison; Imel, Erik A