In vivo gene editing via homology-independent targeted integration for adrenoleukodystrophy treatment
利用同源非依赖性靶向整合进行体内基因编辑治疗肾上腺脑白质营养不良症
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2021.05.022
Hong, Sung-Ah; Seo, Jung Hwa; Wi, Soohyun; Jung, Eul Sik; Yu, Jihyeon; Hwang, Gue-Ho; Yu, Ji Hea; Baek, Ahreum; Park, Soeon; Bae, Sangsu; Cho, Sung-Rae
