Effects of enzyme replacement therapy in sibling cases of hypophosphatasia of varying severities
酶替代疗法对不同严重程度的低磷酸酶症同胞患者的影响
期刊:Clinical Pediatric Endocrinology
影响因子:1.2
doi:10.1297/cpe.2024-0084
Kanno, Junko; Nakagawa, Tomohiro; Miura, Akinobu; Shima, Hirohito; Sogi, Chisumi; Kamimura, Miki; Fujiwara, Ikuma; Tachikawa, Kanako; Hino, Ryoko; Michigami, Toshimi; Kikuchi, Atsuo